Analysis of disease model iPSCs derived from patients with a novel Fanconi anemia-like IBMFS ADH5/ALDH2 deficiency
对患有新型范康尼贫血症样 IBMFS ADH5/ALDH2 缺乏症的患者衍生的疾病模型 iPSC 进行分析
期刊:Blood
影响因子:21
doi:10.1182/blood.2020009111
Anfeng Mu, Asuka Hira, Akira Niwa, Mitsujiro Osawa, Kenichi Yoshida, Minako Mori, Yusuke Okamoto, Kazuko Inoue, Keita Kondo, Masato T Kanemaki, Tomonari Matsuda, Etsuro Ito, Seiji Kojima, Tatsutoshi Nakahata, Seishi Ogawa, Keigo Tanaka, Keitaro Matsuo, Megumu K Saito, Minoru Takata