Preclinical characterization of antagomiR-218 as a potential treatment for myotonic dystrophy
antagomiR-218 作为强直性肌营养不良症潜在治疗方法的临床前表征
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.5
doi:10.1016/j.omtn.2021.07.017
Estefanía Cerro-Herreros, Irene González-Martínez, Nerea Moreno, Jorge Espinosa-Espinosa, Juan M Fernández-Costa, Anna Colom-Rodrigo, Sarah J Overby, David Seoane-Miraz, Javier Poyatos-García, Juan J Vilchez, Adolfo López de Munain, Miguel A Varela, Matthew J Wood, Manuel Pérez-Alonso, Beatriz Llamu