日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Anakinra in Sanfilippo syndrome: a phase 1/2 trial

阿纳白滞素在 Sanfilippo 综合征中的应用:一项 1/2 期临床试验

Lynda E Polgreen, Agnes H Chen, Youngju Pak, Anna Luzzi, Adolfo Morales Garval, Jonathan Acevedo, Gal Bitan, Michelina Iacovino, Cara O'Neill, Julie B Eisengart

Skeletal muscle cell protein dysregulation highlights the pathogenesis mechanism of myopathy-associated p97/VCP R155H mutations

骨骼肌细胞蛋白失调凸显肌病相关 p97/VCP R155H 突变的发病机制

Anna Luzzi, Feng Wang, Shan Li, Michelina Iacovino, Tsui-Fen Chou

Brain transplantation of genetically corrected Sanfilippo type B neural stem cells induces partial cross-correction of the disease

基因修正的 Sanfilippo B 型神经干细胞的脑移植可诱导疾病的部分交叉校正

Yewande Pearse, Don Clarke, Shih-Hsin Kan, Steven Q Le, Valentina Sanghez, Anna Luzzi, Ivy Pham, Lina R Nih, Jonathan D Cooper, Patricia I Dickson, Michelina Iacovino

Notch activation is required for downregulation of HoxA3-dependent endothelial cell phenotype during blood formation

Notch 激活是血液形成过程中 HoxA3 依赖性内皮细胞表型下调的必要条件

Valentina Sanghez, Anna Luzzi, Don Clarke, Dustin Kee, Steven Beuder, Danielle Rux, Mitsujiro Osawa, Joaquín Madrenas, Tsui-Fen Chou, Michael Kyba, Michelina Iacovino

HIV-1 Tat induces DNMT over-expression through microRNA dysregulation in HIV-related non Hodgkin lymphomas

HIV-1 Tat 通过 microRNA 失调诱导 HIV 相关非霍奇金淋巴瘤中的 DNMT 过度表达

Anna Luzzi, Federica Morettini, Sara Gazaneo, Lucia Mundo, Anna Onnis, Susanna Mannucci, Emily A Rogena, Cristiana Bellan, Lorenzo Leoncini, Giulia De Falco