Preclinical evaluation of efficacy and safety of an improved lentiviral vector for the treatment of β-thalassemia and sickle cell disease
改良慢病毒载体治疗β地中海贫血和镰状细胞病的疗效和安全性的临床前评估
期刊:Current Gene Therapy
影响因子:3.8
doi:10.2174/1566523214666141127095336
Olivier Negre, Cynthia Bartholomae, Yves Beuzard, Marina Cavazzana, Lauryn Christiansen, Céline Courne, Annette Deichmann, Maria Denaro, Edouard de Dreuzy, Mitchell Finer, Raffaele Fronza, Béatrix Gillet-Legrand, Christophe Joubert, Robert Kutner, Philippe Leboulch, Leïla Maouche, Anaïs Paulard, Fra