Preclinical evaluation of antisense oligonucleotide therapy in a mouse model of HNRNPH2-related neurodevelopmental disorder
在HNRNPH2相关神经发育障碍小鼠模型中对反义寡核苷酸疗法进行临床前评估
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影响因子:
doi:10.1101/2025.11.04.686541
Korff, Ane; Yang, Xiaojing; Ozdemir, Ozan; Samanta, Ananya; Wang, Yong-Dong; Patni, Tushar; Lavado, Alfonso J; Kavirayani, Anoop Murthy; Ochaba, Joseph; Powers, Berit; Bennett, C Frank; Kim, Hong Joo; Taylor, J Paul