Wild-type C9orf72 expression is a genetic modifier of C9-ALS survival
野生型C9orf72表达是C9-ALS生存的遗传修饰因子
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doi:10.64898/2026.02.06.26345684
Tsitkov, Stanislav; Raju, Akshay; Wu, Jie; Li, Jonathan; Lim, Ryan G; Wu, Zhuoxing; Bistami, Noura Al; Consortium, Answer Als; Van Eyk, Jennifer E; Svendsen, Clive N; Rothstein, Jeffrey D; Glass, Jonathan D; Finkbeiner, Steve; Kaye, Julia A; Thompson, Leslie M; Fraenkel, Ernest