Delivery is key: lessons learnt from developing splice-switching antisense therapies
递送是关键：从开发剪接转换反义疗法中汲取的经验教训
期刊:EMBO Molecular Medicine
影响因子:8.3
doi:10.15252/emmm.201607199
Godfrey, Caroline; Desviat, Lourdes R; Smedsrød, Bård; Piétri-Rouxel, France; Denti, Michela A; Disterer, Petra; Lorain, Stéphanie; Nogales-Gadea, Gisela; Sardone, Valentina; Anwar, Rayan; El Andaloussi, Samir; Lehto, Taavi; Khoo, Bernard; Brolin, Camilla; van Roon-Mom, Willeke Mc; Goyenvalle, Aurélie; Aartsma-Rus, Annemieke; Arechavala-Gomeza, Virginia
