Structural basis of liver de-targeting and neuronal tropism of CNS-targeted AAV capsids.
中枢神经系统靶向AAV衣壳的肝脏去靶向性和神经元趋向性的结构基础
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doi:10.1101/2025.06.02.655683
Brittain Tyler J, Jang Seongmin, Coughlin Gerard M, Barcelona Bre'Anna H, Giriat Izabela, Ristic Fiona, Appling Nathan, Chossis Camille Pma, Shay Timothy F, Gradinaru Viviana