Virally delivered channelrhodopsin-2 safely and effectively restores visual function in multiple mouse models of blindness
病毒载体递送的通道视紫红质-2能够安全有效地恢复多种小鼠失明模型的视觉功能。
期刊:Molecular Therapy
影响因子:12
doi:10.1038/mt.2011.69
Doroudchi, M Mehdi; Greenberg, Kenneth P; Liu, Jianwen; Silka, Kimberly A; Boyden, Edward S; Lockridge, Jennifer A; Arman, A Cyrus; Janani, Ramesh; Boye, Shannon E; Boye, Sanford L; Gordon, Gabriel M; Matteo, Benjamin C; Sampath, Alapakkam P; Hauswirth, William W; Horsager, Alan