A Phase II Trial of Guadecitabine in Children and Adults with SDH-Deficient GIST, Pheochromocytoma, Paraganglioma, and HLRCC-Associated Renal Cell Carcinoma
一项针对患有SDH缺陷型胃肠道间质瘤、嗜铬细胞瘤、副神经节瘤和HLRCC相关肾细胞癌的儿童和成人患者的Guadecitabine II期临床试验
期刊:Clinical Cancer Research
影响因子:10.2
doi:10.1158/1078-0432.CCR-22-2168
Ligon, John A; Sundby, R Taylor; Wedekind, Mary F; Arnaldez, Fernanda I; Del Rivero, Jaydira; Wiener, Lori; Srinivasan, Ramaprasad; Spencer, Melissa; Carbonell, Amanda; Lei, Haiyan; Shern, John; Steinberg, Seth M; Figg, William D; Peer, Cody J; Zimmerman, Sara; Moraly, Josquin; Xu, Xia; Fox, Stephen; Chan, King; Barbato, Michael I; Andresson, Thorkell; Taylor, Naomi; Pacak, Karel; Killian, J Keith; Dombi, Eva; Linehan, W Marston; Miettinen, Markku; Piekarz, Richard; Helman, Lee J; Meltzer, Paul; Widemann, Brigitte; Glod, John