日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Loss of factor VIII in zebrafish rebalances antithrombin deficiency but has a limited bleeding diathesis

斑马鱼体内因子VIII的缺失可以重新平衡抗凝血酶缺乏症,但出血倾向有限。

Raghunath, Azhwar; Richter, Catherine E; Griffin, Megan S; Emly, Sylvia M; Yaman, Murat; Arruda, Valder R; Samelson-Jones, Benjamin J; Shavit, Jordan A

Ancient origin of the furin sequence in the wolf F8 gene

狼F8基因中弗林蛋白酶序列的古老起源

Siner, Joshua I; Barber-Meyer, Shannon; Samelson-Jones, Benjamin J; Mech, Lucyan David; Arruda, Valder R; Crudele, Julie M

AAV gene therapy in companion dogs with severe hemophilia: Real-world long-term data on immunogenicity, efficacy, and quality of life

针对患有严重血友病的伴侣犬的AAV基因疗法:关于免疫原性、疗效和生活质量的真实世界长期数据

Doshi, Bhavya S; Samelson-Jones, Benjamin J; Nichols, Timothy C; Merricks, Elizabeth P; Siner, Joshua L; French, Robert A; Lee, Ben J; Arruda, Valder R; Callan, Mary Beth

Characteristics of BAY 2599023 in the Current Treatment Landscape of Hemophilia A Gene Therapy

BAY 2599023 在当前 A 型血友病基因治疗治疗格局中的特征

Pipe, Steven W; Arruda, Valder R; Lange, Claudia; Kitchen, Stephen; Eichler, Hermann; Wadsworth, Samuel

Immune complications and their management in inherited and acquired bleeding disorders

遗传性和获得性出血性疾病的免疫并发症及其治疗

Arruda, Valder R; Lillicrap, David; Herzog, Roland W

B cell-activating factor modulates the factor VIII immune response in hemophilia A.

B 细胞激活因子调节 A 型血友病中的 VIII 因子免疫反应

Doshi Bhavya S, Rana Jyoti, Castaman Giancarlo, Shaheen Mostafa A, Kaczmarek Radoslaw, Butterfield John Ss, Meeks Shannon L, Leissinger Cindy, Biswas Moanaro, Arruda Valder R

Why is AAV FVIII gene therapy not approved by the US Food and Drug Administration yet?

为什么AAV FVIII基因疗法至今尚未获得美国食品药品监督管理局的批准?

Arruda, Valder R

Evolutionary insights into coagulation factor IX Padua and other high-specific-activity variants

对凝血因子IX Padua和其他高比活性变体的进化见解

Samelson-Jones, Benjamin J; Finn, Jonathan D; Raffini, Leslie J; Merricks, Elizabeth P; Camire, Rodney M; Nichols, Timothy C; Arruda, Valder R

Gene Therapy for Inherited Bleeding Disorders

基因疗法治疗遗传性出血性疾病

Arruda, Valder R; Weber, Jesse; Samelson-Jones, Benjamin J

Translational Potential of Immune Tolerance Induction by AAV Liver-Directed Factor VIII Gene Therapy for Hemophilia A

AAV肝脏靶向因子VIII基因疗法诱导免疫耐受治疗A型血友病的转化潜力

Samelson-Jones, Benjamin J; Arruda, Valder R