日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Lentiviral Vectors for Ocular Gene Therapy

用于眼部基因治疗的慢病毒载体

Arsenijevic, Yvan; Berger, Adeline; Udry, Florian; Kostic, Corinne

Enhancer of Zeste Homolog 2 (EZH2) Contributes to Rod Photoreceptor Death Process in Several Forms of Retinal Degeneration and Its Activity Can Serve as a Biomarker for Therapy Efficacy.

Zeste同源物2增强子(EZH2)在多种视网膜变性中促进视杆感光细胞死亡过程,其活性可作为治疗效果的生物标志物

Mbefo Martial, Berger Adeline, Schouwey Karine, Gérard Xavier, Kostic Corinne, Beryozkin Avigail, Sharon Dror, Dolfuss Hélène, Munier Francis, Tran Hoai Viet, van Lohuizen Maarten, Beltran William A, Arsenijevic Yvan

Pharmacological disruption of the Notch transcription factor complex

Notch转录因子复合物的药理学破坏

Lehal, Rajwinder; Zaric, Jelena; Vigolo, Michele; Urech, Charlotte; Frismantas, Viktoras; Zangger, Nadine; Cao, Linlin; Berger, Adeline; Chicote, Irene; Loubéry, Sylvain; Choi, Sung Hee; Koch, Ute; Blacklow, Stephen C; Palmer, Hector G; Bornhauser, Beat; González-Gaitán, Marcos; Arsenijevic, Yvan; Zoete, Vincent; Aster, Jon C; Bourquin, Jean-Pierre; Radtke, Freddy

Gene Transfer with AAV9-PHP.B Rescues Hearing in a Mouse Model of Usher Syndrome 3A and Transduces Hair Cells in a Non-human Primate

利用 AAV9-PHP.B 进行基因转移可挽救 Usher 综合征 3A 小鼠模型的听力,并转导非人灵长类动物的毛细胞。

György, Bence; Meijer, Elise J; Ivanchenko, Maryna V; Tenneson, Kelly; Emond, Frederick; Hanlon, Killian S; Indzhykulian, Artur A; Volak, Adrienn; Karavitaki, K Domenica; Tamvakologos, Panos I; Vezina, Mark; Berezovskii, Vladimir K; Born, Richard T; O'Brien, Maureen; Lafond, Jean-François; Arsenijevic, Yvan; Kenna, Margaret A; Maguire, Casey A; Corey, David P

Animal modelling for inherited central vision loss

遗传性中心视力丧失的动物模型

Kostic, Corinne; Arsenijevic, Yvan

Determination of Rod and Cone Influence to the Early and Late Dynamic of the Pupillary Light Response

确定视杆细胞和视锥细胞对瞳孔光反应早期和晚期动态的影响

Kostic, Corinne; Crippa, Sylvain V; Martin, Catherine; Kardon, Randy H; Biel, Martin; Arsenijevic, Yvan; Kawasaki, Aki

Amyloid Precursor-Like Protein 2 deletion-induced retinal synaptopathy related to congenital stationary night blindness: structural, functional and molecular characteristics

淀粉样前体蛋白样蛋白2缺失诱导的视网膜突触病变与先天性静止性夜盲症相关:结构、功能和分子特征

Dinet, Virginie; Ciccotosto, Giuseppe D; Delaunay, Kimberley; Borras, Céline; Ranchon-Cole, Isabelle; Kostic, Corinne; Savoldelli, Michèle; El Sanharawi, Mohamed; Jonet, Laurent; Pirou, Caroline; An, Na; Abitbol, Marc; Arsenijevic, Yvan; Behar-Cohen, Francine; Cappai, Roberto; Mascarelli, Frédéric

Adamts18 deletion results in distinct developmental defects and provides a model for congenital disorders of lens, lung, and female reproductive tract development

Adamts18基因缺失会导致明显的发育缺陷,并为晶状体、肺和女性生殖道发育的先天性疾病提供了一个模型。

Ataca, Dalya; Caikovski, Marian; Piersigilli, Alessandra; Moulin, Alexandre; Benarafa, Charaf; Earp, Sarah E; Guri, Yakir; Kostic, Corinne; Arsenijevic, Yvan; Soininen, Raija; Apte, Suneel S; Brisken, Cathrin

Derivation of traceable and transplantable photoreceptors from mouse embryonic stem cells

从小鼠胚胎干细胞中衍生出可追踪和可移植的光感受器

Decembrini, Sarah; Koch, Ute; Radtke, Freddy; Moulin, Alexandre; Arsenijevic, Yvan

Rapid cohort generation and analysis of disease spectrum of large animal model of cone dystrophy

快速构建队列并分析大型动物视锥细胞营养不良模型的疾病谱

Kostic, Corinne; Lillico, Simon Geoffrey; Crippa, Sylvain Vincent; Grandchamp, Nicolas; Pilet, Héloïse; Philippe, Stéphanie; Lu, Zen; King, Tim James; Mallet, Jacques; Sarkis, Chamsy; Arsenijevic, Yvan; Whitelaw, Christopher Bruce Alexander