日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Stathmin-2 enhances motor axon regeneration after injury independent of its binding to tubulin

Stathmin-2 可促进损伤后运动轴突的再生,且该作用独立于其与微管蛋白的结合。

Beccari, Melinda S; Arnold-Garcia, Olatz; Baughn, Michael W; Artates, Jonathan W; McAlonis-Downes, Melissa; Lim, Jaisen; Leyva-Cázares, Dulce Fernanda; Rubio-Lara, Hugo Isaac; Ramirez-Rodriguez, Andrea; Bernal-Buenrostro, Carol N; Murgia-Bay, Brian; Rangel, Carolina K; Kim, Dong Hyun; Melamed, Ze'ev; Lutz, Cathleen M; Lagier-Tourenne, Clotilde; Corbett, Kevin D; López-Erauskin, Jone; Cleveland, Don W

Dual-targeting snRNA gene therapy rescues STMN2 and UNC13A splicing in TDP-43 proteinopathies

双靶向snRNA基因疗法可挽救TDP-43蛋白病中的STMN2和UNC13A剪接

Gomberg, Trent A; Elmsaouri, Sara; Kopalle, Hema M; Baughn, Michael W; Beccari, Melinda S; McAlonis-Downes, Melissa; Artates, Jonathan W; Pant, Deepak; Mak, Harriet; Smargon, Aaron A; Sander, Tynan C; Garcia, Esaul; Lee, Dominic P; Cleveland, Don W; Yeo, Gene W

Stathmin-2 loss leads to neurofilament-dependent axonal collapse driving motor and sensory denervation

Stathmin-2 的缺失会导致神经丝依赖性轴突塌陷,进而引发运动和感觉神经支配丧失。

López-Erauskin, Jone; Bravo-Hernandez, Mariana; Presa, Maximiliano; Baughn, Michael W; Melamed, Ze'ev; Beccari, Melinda S; Agra de Almeida Quadros, Ana Rita; Arnold-Garcia, Olatz; Zuberi, Aamir; Ling, Karen; Platoshyn, Oleksandr; Niño-Jara, Elkin; Ndayambaje, I Sandra; McAlonis-Downes, Melissa; Cabrera, Larissa; Artates, Jonathan W; Ryan, Jennifer; Hermann, Anita; Ravits, John; Bennett, C Frank; Jafar-Nejad, Paymaan; Rigo, Frank; Marsala, Martin; Lutz, Cathleen M; Cleveland, Don W; Lagier-Tourenne, Clotilde

Exploring the effect of sequence length and composition on allele-selective inhibition of human huntingtin expression by single-stranded silencing RNAs.

探索序列长度和组成对单链沉默RNA选择性抑制人类亨廷顿蛋白表达的影响

Hu Jiaxin, Liu Jing, Yu Dongbo, Aiba Yuichiro, Lee Suheung, Pendergraff Hannah, Boubaker Jihane, Artates Jonathan W, Lagier-Tourenne Clotilde, Lima Walt F, Swayze Eric E, Prakash Thazha P, Corey David R

Sustained therapeutic reversal of Huntington's disease by transient repression of huntingtin synthesis

通过暂时抑制亨廷顿蛋白合成,实现亨廷顿病的持续治疗性逆转。

Kordasiewicz, Holly B; Stanek, Lisa M; Wancewicz, Edward V; Mazur, Curt; McAlonis, Melissa M; Pytel, Kimberly A; Artates, Jonathan W; Weiss, Andreas; Cheng, Seng H; Shihabuddin, Lamya S; Hung, Gene; Bennett, C Frank; Cleveland, Don W