日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Optimal SpCas9- and SaCas9-mediated gene editing by enhancing gRNA transcript levels through scaffold poly-T tract reduction

通过减少支架多聚T序列来提高gRNA转录水平,从而优化SpCas9和SaCas9介导的基因编辑。

Chey, Yu C J; Gierus, Luke; Lushington, Caleb; Arudkumar, Jayshen C; B Geiger, Ashleigh; Staker, Lachlan G; Robertson, Louise J; Pfitzner, Chandran; Kennedy, Jesse G; Lee, Ryan H B; Godahewa, Gelshan I; Adikusuma, Fatwa; Thomas, Paul Q

CRISPR-mediated megabase-scale transgene de-duplication to generate a functional single-copy full-length humanized DMD mouse model

CRISPR 介导的百万碱基规模转基因去重复生成功能性单拷贝全长人源化 DMD 小鼠模型

Yu C J Chey, Mark A Corbett, Jayshen Arudkumar, Sandra G Piltz, Paul Q Thomas, Fatwa Adikusuma

CRISPR applications for Duchenne muscular dystrophy: From animal models to potential therapies

CRISPR技术在杜氏肌营养不良症中的应用:从动物模型到潜在疗法

Chey, Yu C J; Arudkumar, Jayshen; Aartsma-Rus, Annemieke; Adikusuma, Fatwa; Thomas, Paul Q

Optimized nickase- and nuclease-based prime editing in human and mouse cells

在人和小鼠细胞中优化基于切口酶和核酸酶的先导编辑

Adikusuma, Fatwa; Lushington, Caleb; Arudkumar, Jayshen; Godahewa, Gelshan I; Chey, Yu C J; Gierus, Luke; Piltz, Sandra; Geiger, Ashleigh; Jain, Yatish; Reti, Daniel; Wilson, Laurence O W; Bauer, Denis C; Thomas, Paul Q