Gene Editing for CEP290-Associated Retinal Degeneration
基因编辑治疗CEP290相关视网膜变性
期刊:New England Journal of Medicine
影响因子:78.5
doi:10.1056/NEJMoa2309915
Pierce, Eric A; Aleman, Tomas S; Jayasundera, Kanishka T; Ashimatey, Bright S; Kim, Keunpyo; Rashid, Alia; Jaskolka, Michael C; Myers, Rene L; Lam, Byron L; Bailey, Steven T; Comander, Jason I; Lauer, Andreas K; Maguire, Albert M; Pennesi, Mark E