日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

In vivo site-specific engineering to reprogram T cells

利用体内位点特异性工程技术重编程T细胞

Nyberg, William A; Bernard, Pierre-Louis; Ngo, Wayne; Wang, Charlotte H; Ark, Jonathan; Rothrock, Allison; Borgo, Gina M; Kimmerly, Gabriella R; Jung, Jae Hyung; Allain, Vincent; Hamilton, Jennifer R; Baldwin, Alisha; Stickels, Robert; Wyman, Sarah; Khan, Safwaan H; Lang, Shanshan; Marsh, Donna; Almudhfar, Niran; Novick, Catherine; Mortazavi, Yasaman; Zhang, Shimin; AbdElwakil, Mahmoud M; Sandoval, Luis R; Hwang, Sidney; Chu, Simon N; Jung, Hyuncheol; Liu, Chang; Sharma, Devesh; McCreary, Travis; Li, Zhongmei; Satpathy, Ansuman T; Carnevale, Julia; Rutishauser, Rachel L; Cromer, M Kyle; Roybal, Kole T; Dodgson, Stacie E; Doudna, Jennifer A; Asokan, Aravind; Eyquem, Justin

Enhancer-directed gene delivery for digit regeneration based on conserved epidermal factors

基于保守表皮因子的增强子导向基因递送用于手指再生

Brown, David A; Koll, Katja K; Brush, Erin; Darner, Grant; Curtis, Timothy Jr; Dvergsten, Thomas; Tran, Melissa; Milligan, Colleen; Wolfson, David W; Gonzalez, Trevor J; Jeffs, Sydney; Ehrhardt, Alyssa; Bitolas, Rochelle; Landau, Madeleine; Reitz, Kendall; Salven, David S; Slota-Burtt, Leslie A; Snee, Isabel; Singer-Freeman, Elena; Bhatia, Sayuri; Ou, Jianhong; Asokan, Aravind; Currie, Joshua D; Poss, Kenneth D

Rewriting Renal Fate: The Evolving Landscape of Adeno-Associated Virus-Mediated Kidney Gene Therapies

改写肾脏命运:腺相关病毒介导的肾脏基因疗法的演变格局

Hickman, Peyton G; Asokan, Aravind; Wilson, Matthew H

Liver-directed AAV gene therapy in mice corrects glycogen storage disease type IX γ2

小鼠肝脏靶向AAV基因疗法可纠正糖原贮积症IX型γ2

Gibson, Rebecca A; Jeck, William R; Koch, Rebecca L; Jumani, Neha; Choi, Su Jin; Bali, Deeksha; Young, Sarah P; Asokan, Aravind; Lim, Jeong-A; Kishnani, Priya S

Complete neutralizing antibody evasion by serodivergent non-mammalian AAVs enables gene therapy redosing

血清型不同的非哺乳动物腺相关病毒(AAV)能够完全逃避中和抗体,从而实现基因治疗的重复给药。

Loeb, Ezra J; Fergione, Sophia A; Yudistyra, Vivian; Fanous, Marco M; Benkert, Abigail R; Fisher, Delaney G; Hull, Joshua A; ElMallah, Mai K; Asokan, Aravind

Spatial and longitudinal tracking of enhancer-AAV vectors that target transgene expression to injured mouse myocardium

对靶向转基因表达至受损小鼠心肌的增强子-AAV载体进行空间和纵向追踪

Wolfson, David W; Hull, Joshua A; Li, Yongwu; Gonzalez, Trevor J; Jayaram, Mourya D; Devlin, Garth W; Cigliola, Valentina; Oonk, Kelsey A; Rosales, Alan; Bursac, Nenad; Asokan, Aravind; Poss, Kenneth D

Deletion of Exon 51 in a Humanized Duchenne Muscular Dystrophy Mouse Model Abolishes Ventricular Arrhythmia Predisposition

在人源化杜氏肌营养不良症小鼠模型中,删除第51号外显子可消除室性心律失常易感性

Perelli, Robin M; Sitton, Madeleine J; Bohning, Joel D; Pickar-Oliver, Adrian; McCullough, K Tyler; Moya-Mendez, Mary E; Zheng, Scott; Daniels, Heather; Devlin, Garth; Asokan, Aravind; Gersbach, Charles A; Landstrom, Andrew P

Efficient kidney gene transfer and proximal tubule transduction using self-complementary AAV.cc47 vectors.

利用自互补 AAV.cc47 载体实现高效的肾脏基因转移和近端肾小管转导。

Peek Jennifer L, Rosales Alan, Qi Julie, Feleke Lena, Menshikh Anna, Welch Richard C, Woodard Lauren E, Asokan Aravind, Wilson Matthew H

Probing aspects of extracellular vesicle associated AAV allows increased vector yield and insight into its transduction and immune-evasive properties.

探究与细胞外囊泡相关的 AAV 的各个方面,可以提高载体产量,并深入了解其转导和免疫逃避特性

Cheng Ming, Cruz Demitri de la, Crain Adam V, Espinoza Paula, Ng Carrie, Elmore Zachary C, Asokan Aravind, Maguire Casey A

Evaluation of AAV Capsids and Delivery Approaches for Hereditary Hemorrhagic Telangiectasia Gene Therapy.

遗传性出血性毛细血管扩张症基因治疗中AAV衣壳和递送方法的评估

Yadav Alka, Liang Rich, Press Kelly, Schmidt Annika, Shabani Zahra, Leng Kun, Wang Calvin, Sekhar Abinav, Shi Joshua, Devlin Garth W, Gonzalez Trevor J, Asokan Aravind, Su Hua