Cytosine base editing of LPA in transgenic mice averts large deletions.
对转基因小鼠中LPA的胞嘧啶碱基进行编辑可以避免大片段缺失。
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2026.02.049
Chuecos Marcel A, Park So Hyun, Bhakta Madhvi M, Too-Chiobi Usosa, Betancourth Daniel, Cao Mingming, De Giorgi Marco, Walkey Christopher J, Tiwari Anjana, Godin Biana, Assini Julia M, Palmer Donna J, Ng Philip, Boffa Michael B, Koschinsky Marlys L, Bao Gang, Lagor William R