日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Generation of human induced pluripotent stem cell lines from patients with PHACE syndrome

从PHACE综合征患者中生成人类诱导多能干细胞系

Ramchandani, Rohin; Cheawsamoot, Chanatjit; Torres, Giovanni A; Arthur Ataam, Jennifer; Siegel, Dawn; Karakikes, Ioannis

Empagliflozin Attenuates Arrhythmias in an iPSC-Based Model of Hypertrophic Cardiomyopathy

恩格列净可减轻基于iPSC的肥厚型心肌病模型中的心律失常

Arthur Ataam, Jennifer; Belbachir, Nadjet; Perea-Gil, Isaac; Termglinchan, Vittavat; Vadgama, Nirmal; Garg, Priyanka; Ramchandani, Rohin; Gavidia, Alexandra A; Roura, Santiago; Gálvez-Montón, Carolina; Wu, Joseph C; Bayés-Genis, Antoni; Karakikes, Ioannis

Non-viral in vivo cytidine base editing in hepatocytes using focused ultrasound targeted microbubbles.

利用聚焦超声靶向微泡在肝细胞中进行非病毒体内胞嘧啶碱基编辑

Anderson Cynthia D, Arthur Jennifer Ataam, Zhang Yuan, Bharucha Nike, Karakikes Ioannis, Shohet Ralph V

Targeting mAKAPβ expression as a therapeutic approach for ischemic cardiomyopathy

以mAKAPβ表达为靶点治疗缺血性心肌病

Martinez, Eliana C; Li, Jinliang; Ataam, Jennifer Arthur; Tokarski, Kristin; Thakur, Hrishikesh; Karakikes, Ioannis; Dodge-Kafka, Kimberly; Kapiloff, Michael S

Generation of human induced pluripotent stem cell lines derived from four patients with a pathogenic ALPK3 variant associated with adult-onset hypertrophic cardiomyopathy (HCM)

利用四名携带与成人发病型肥厚型心肌病 (HCM) 相关的致病性 ALPK3 变异的患者,生成人类诱导多能干细胞系

Cheawsamoot, Chanatjit; Ramchandani, Rohin; Ameen, Mohamed; Arthur Ataam, Jennifer; Khongphatthanayothin, Apichai; Shotelersuk, Vorasuk; Karakikes, Ioannis

Serine biosynthesis as a novel therapeutic target for dilated cardiomyopathy

丝氨酸生物合成作为扩张型心肌病的新型治疗靶点

Perea-Gil, Isaac; Seeger, Timon; Bruyneel, Arne A N; Termglinchan, Vittavat; Monte, Emma; Lim, Esther W; Vadgama, Nirmal; Furihata, Takaaki; Gavidia, Alexandra A; Arthur Ataam, Jennifer; Bharucha, Nike; Martinez-Amador, Noel; Ameen, Mohamed; Nair, Pooja; Serrano, Ricardo; Kaur, Balpreet; Feyen, Dries A M; Diecke, Sebastian; Snyder, Michael P; Metallo, Christian M; Mercola, Mark; Karakikes, Ioannis

Generation of a dual edited human induced pluripotent stem cell Myl7-GFP reporter line with inducible CRISPRi/dCas9

生成具有可诱导 CRISPRi/dCas9 的双重编辑人类诱导多能干细胞 Myl7-GFP 报告系

Eyal Metzl-Raz, Nike Bharucha, Jennifer Arthur Ataam, Alexandra A Gavidia, William J Greenleaf, Ioannis Karakikes

Unfolded Protein Response as a Compensatory Mechanism and Potential Therapeutic Target in PLN R14del Cardiomyopathy

未折叠蛋白反应作为PLN R14del心肌病的一种代偿机制和潜在治疗靶点

Feyen, Dries A M; Perea-Gil, Isaac; Maas, Renee G C; Harakalova, Magdalena; Gavidia, Alexandra A; Arthur Ataam, Jennifer; Wu, Ting-Hsuan; Vink, Aryan; Pei, Jiayi; Vadgama, Nirmal; Suurmeijer, Albert J; Te Rijdt, Wouter P; Vu, Michelle; Amatya, Prashila L; Prado, Maricela; Zhang, Yuan; Dunkenberger, Logan; Sluijter, Joost P G; Sallam, Karim; Asselbergs, Folkert W; Mercola, Mark; Karakikes, Ioannis

Targeted proteomics of right heart adaptation to pulmonary arterial hypertension

针对右心适应肺动脉高压的靶向蛋白质组学研究

Amsallem, Myriam; Sweatt, Andrew J; Arthur Ataam, Jennifer; Guihaire, Julien; Lecerf, Florence; Lambert, Mélanie; Ghigna, Maria Rosa; Ali, Md Khadem; Mao, Yuqiang; Fadel, Elie; Rabinovitch, Marlene; de Jesus Perez, Vinicio; Spiekerkoetter, Edda; Mercier, Olaf; Haddad, Francois; Zamanian, Roham T

Generation of AAVS1 integrated doxycycline-inducible CRISPR-Prime Editor human induced pluripotent stem cell line

构建AAVS1整合的强力霉素诱导型CRISPR-Prime编辑器人诱导多能干细胞系

Bharucha, Nike; Ataam, Jennifer Arthur; Gavidia, Alexandra A; Karakikes, Ioannis