Riociguat in patients with sickle cell disease and hypertension or proteinuria (STERIO-SCD): a randomised, double-blind, placebo controlled, phase 1-2 trial
利奥西呱治疗伴有高血压或蛋白尿的镰状细胞病患者(STERIO-SCD):一项随机、双盲、安慰剂对照的1/2期试验
期刊:Lancet Haematology
影响因子:17.7
doi:10.1016/S2352-3026(24)00045-0
Gladwin, Mark T; Gordeuk, Victor R; Desai, Payal C; Minniti, Caterina; Novelli, Enrico M; Morris, Claudia R; Ataga, Kenneth I; De Castro, Laura; Curtis, Susanna A; El Rassi, Fuad; Ford, Hubert James; Harrington, Thomas; Klings, Elizabeth S; Lanzkron, Sophie; Liles, Darla; Little, Jane; Nero, Alecia; Smith, Wally; Taylor, James G 6th; Baptiste, Ayanna; Hagar, Ward; Kanter, Julie; Kinzie, Amy; Martin, Temeia; Rafique, Amina; Telen, Marilyn J; Lalama, Christina M; Kato, Gregory J; Abebe, Kaleab Z