日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

One Shock, Not One Cure: Electroporation Reveals Disease-Specific Constraints in Hepatocyte Gene Editing Therapy.

一次电击,而非一次治愈:电穿孔揭示肝细胞基因编辑疗法中疾病特异性限制

Clark Callie, Pokhrel Menam, Arthur Benjamin, Suresh Pramita, Ates Ilayda, Gibson Justin, Dhungana Abishek, Mehlem Ryan, Boysia Andrew, Padalkar Mugdha V, Pokhrel Achala, Echesabal-Chen Jing, Vonada Anne, Stamatikos Alexis, Savinova Olga V, Grompe Markus, Cottle Renee N

Ex vivo gene editing and cell therapy for hereditary tyrosinemia type 1

体外基因编辑和细胞疗法治疗1型遗传性酪氨酸血症

Ates, Ilayda; Stuart, Callie; Rathbone, Tanner; Barzi, Mercedes; He, Gordon; Major, Angela M; Shankar, Vijay; Lyman, Rachel A; Angner, Sidney S; Mackay, Trudy F C; Srinivasan, Shanthi; Farris, Alton Brad; Bissig, Karl-Dimiter; Cottle, Renee N

Delivery Approaches for Therapeutic Genome Editing and Challenges

治疗性基因组编辑的递送方法及挑战

Ates, Ilayda; Rathbone, Tanner; Stuart, Callie; Bridges, P Hudson; Cottle, Renee N