In utero lipid nanoparticle delivery achieves robust editing in hematopoietic stem cells.
子宫内脂质纳米颗粒递送可实现对造血干细胞的强效编辑
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doi:10.1101/2025.05.12.652147
Worthington Atesh K, Borges Beltran, Lum Tony, Echeverri Elisa Schrader, Zada Fareha Moulana, Cordero Marco A, Kim Hyejin, Zenhausern Ryan, Celik Ozgenur, Shaw Cindy, Gutierrez-Martinez Paula, Omarova Marzhana, Blanchard Chris, Burns Sean, Cromer M Kyle, Dahlman James E, MacKenzie Tippi C