Sensitivity of Different Clinical Outcome Measures in Assessing Adults With Becker Muscular Dystrophy: A 3-Year Natural History Study
不同临床结局指标在评估贝克尔型肌营养不良症成人患者中的敏感性:一项为期3年的自然史研究
期刊:Neurology
影响因子:8.5
doi:10.1212/WNL.0000000000214071
Schrama, Esther J; Koeks, Zaïda; Van De Velde, Nienke M; Alleman, Iris; van Benthem, Jules J; van Weperen, Pieteke W; Hooijmans, Melissa T; Kan, Hermien E; Spitali, Pietro; Ajmone Marsan, Nina; Atsma, Douwe E; van Duyvenvoorde, Hermine A; Verschuuren, Jan J G M; Niks, Erik H