Motor Function in Limb-Girdle Muscular Dystrophy R1/2A: Validation of Clinical Outcome Assessments for Clinical Care and Trial Readiness
肢带型肌营养不良症 R1/2A 的运动功能:临床护理和试验准备的临床结果评估的验证
期刊:Neurology-Genetics
影响因子:3.7
doi:10.1212/NXG.0000000000200323
James, Meredith K; Iammarino, Megan A; Reash, Natalie F; Steiner, Christopher L; Knight, Audrey B; Smith, Melissa A; Moat, Dionne; Michell-Sodhi, Jassi; Wong, Karen S W; Grover, Emma; Robinson, Emma-Jayne; Mayhew, Anna G; Eagle, Michelle; Elseed, Maha; Guglieri, Michela; Straub, Volker; Marini-Bettolo, Chiara; Muni-Lofra, Robert; Diaz-Manera, Jordi; Lowes, Linda Pax; Alfano, Lindsay N