日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Base edited skin equivalents with clinical potential for ex vivo correction of recessive dystrophic epidermolysis bullosa

具有临床潜力的基础编辑皮肤等效物,可用于体外矫正隐性营养不良性大疱性表皮松解症

Bassons-Bascuñana, Alex; Duarte, Blanca; Méndez-Jiménez, Estela; Ugalde, Laura; Sanabria-Betrián, Paula; Aussel, Clotilde; Peña-Gutiérrez, Irene; Olalla-Sastre, Beatriz; Ammann, Sandra; Cathomen, Toni; Del Rio, Marcela; Río, Paula; Larcher, Fernando; López-Manzaneda, Sergio

Prime editing as a promising therapeutic strategy for junctional epidermolysis bullosa.

Prime编辑作为治疗大疱性交界性表皮松解症的一种有前途的治疗策略。

Hierl Markus, Bischof Johannes, Liemberger Bernadette, Kocher Thomas, Hainzl Stefan, Gruner Stefanie, Trattner Lisa, Reichl Victoria, Klausegger Alfred, Aussel Clotilde, Ammann Sandra, Raab Rebecca, Andrieux Geoffroy, Wolf Martin, Hochmann Sarah, Ebner Patricia, Wally Verena, Zauner Roland, Guttmann-Gruber Christina, Gratz Iris K, Hofbauer Josefina Piñón, Cathomen Toni, Strunk Dirk, Bauer Johann W, Koller Ulrich

Targeted gene editing and near-universal cDNA insertion of CYBA and CYBB as a treatment for chronic granulomatous disease

靶向基因编辑和近乎普遍的 CYBA 和 CYBB cDNA 插入作为慢性肉芽肿病的治疗方法

Wolff, Jonas Holst; Skov, Thomas Wisbech; Haslund, Didde; Dorset, Sofie Rahbek; Revenfeld, Anne Louise S; Aussel, Clotilde; Jørgensen, Sofie E; Holm, Mette; Thomsen, Martin K; Ammann, Sandra; Cathomen, Toni; Mogensen, Trine H; Møller, Bjarne Kuno; Bak, Rasmus O; Mikkelsen, Jacob Giehm

The hidden risks of CRISPR/Cas: structural variations and genome integrity

CRISPR/Cas技术的潜在风险:结构变异和基因组完整性

Aussel, Clotilde; Cathomen, Toni; Fuster-García, Carla

IL-1β primed mesenchymal stromal cells moderate hemorrhagic shock-induced vascular permeability

IL-1β 预处理的间充质基质细胞可减轻出血性休克引起的血管通透性。

Baudry, Nathalie; Campeanu, Aurélie; Aussel, Clotilde; Doutrelon, Caroline; Grosbot, Marion; Banzet, Sébastien; Vicaut, Eric; Peltzer, Juliette

IL-1β primed mesenchymal stromal cells moderate hemorrhagic shock-induced organ injuries.

IL-1β 启动的间充质基质细胞可减轻出血性休克引起的器官损伤

Aussel Clotilde, Baudry Nathalie, Grosbot Marion, Caron Cécile, Vicaut Eric, Banzet Sébastien, Peltzer Juliette