Unravelling genotype-phenotype correlations in Stargardt disease using patient-derived retinal organoids
利用患者来源的视网膜类器官揭示 Stargardt 病的基因型-表型相关性
期刊:Cell Death & Disease
影响因子:8.1
doi:10.1038/s41419-025-07420-7
Avril Watson, Rachel Queen, Luis Ferrández-Peral, Birthe Dorgau, Joseph Collin, Andrew Nelson, Rafiqul Hussain, Jonathan Coxhead, Michael McCorkindale, Robert Atkinson, Darin Zerti, Valeria Chichagova, Ana Conesa, Lyle Armstrong, Frans P M Cremers, Majlinda Lako