Novel AAV capsids for intravitreal gene therapy of photoreceptor disorders
用于玻璃体内基因治疗光感受器疾病的新型 AAV 衣壳
期刊:EMBO Molecular Medicine
影响因子:9
doi:10.15252/emmm.202013392
Marina Pavlou, Christian Schön, Laurence M Occelli, Axel Rossi, Nadja Meumann, Ryan F Boyd, Joshua T Bartoe, Jakob Siedlecki, Maximilian J Gerhardt, Sabrina Babutzka, Jacqueline Bogedein, Johanna E Wagner, Siegfried G Priglinger, Martin Biel, Simon M Petersen-Jones, Hildegard Büning, Stylianos Micha