Assessment of health state utilities associated with adult and pediatric acid sphingomyelinase deficiency (ASMD)
成人和儿童酸性鞘磷脂酶缺乏症 (ASMD) 相关健康状态效用评估
期刊:European Journal of Health Economics
影响因子:3
doi:10.1007/s10198-023-01667-7
Matza, Louis S; Stewart, Katie D; Fournier, Marie; Rowen, Donna; Lachmann, Robin; Scarpa, Maurizio; Mengel, Eugen; Obermeyer, Travis; Ayik, Evren; Laredo, Fernando; Pulikottil-Jacob, Ruth