日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Progress on cell therapy for skeletal muscle disorders

骨骼肌疾病细胞疗法的进展

Azzag, Karim; Perlingeiro, Rita C R

Necessity of Notch3 signaling in myofiber maturation in a pluripotent stem cell transplant model.

在多能干细胞移植模型中,Notch3信号传导对肌纤维成熟是必需的。

Yamashita Aline M S, Crist Sarah B, Garay Bayardo I, Kim Hyunkee, Azzag Karim, Bosnakovski Darko, Faria Sergio H D M, Abrahante Juan E, Abreu Phablo, Ahlquist Aaron, Perlingeiro Rita C R

Preclinical quality, safety, and efficacy of a CGMP iPSC-derived myogenic progenitor product for the treatment of muscular dystrophies.

用于治疗肌营养不良症的 CGMP iPSC 衍生肌源性祖细胞产品的临床前质量、安全性和有效性

Azzag Karim, Magli Alessandro, Kiley James, Sumstad Darin, Kadidlo Diane, Crist Sarah B, Norris Beverly, Ahlquist Aaron, Hocum Stone Laura L, Everett John, Shappa Faustich Jill, Seelig Davis, Rangarajan Parthasarathy, Kim Hyunkee, Flory Craig, Bushman Frederic, Ramachandran Sabarinathan, Kang Peter B, Schumacher Robert J, Wagner John E, Kyba Michael, Graham Melanie L, McKenna David H, Perlingeiro Rita C R

Effect of Notch1 signaling on muscle engraftment and maturation from pluripotent stem cells

Notch1 信号对多能干细胞肌肉植入和成熟的影响

Aline M S Yamashita, Bayardo I Garay, Hyunkee Kim, Darko Bosnakovski, Juan E Abrahante, Karim Azzag, Phablo Abreu, Aaron Ahlquist, Rita C R Perlingeiro

The adult environment promotes the transcriptional maturation of human iPSC-derived muscle grafts

成人环境促进人类 iPSC 衍生肌肉移植物的转录成熟

Sarah B Crist, Karim Azzag, James Kiley, Ilsa Coleman, Alessandro Magli, Rita C R Perlingeiro

A Novel CRISPR-Cas9 Strategy to Target DYSTROPHIN Mutations Downstream of Exon 44 in Patient-Specific DMD iPSCs

一种新型 CRISPR-Cas9 策略,用于靶向患者特异性 DMD iPSC 中外显子 44 下游的肌营养不良蛋白突变

Neha R Dhoke, Hyunkee Kim, Karim Azzag, Sarah B Crist, James Kiley, Rita C R Perlingeiro

Enhanced Diaphragm Muscle Function upon Satellite Cell Transplantation in Dystrophic Mice

营养不良小鼠接受卫星细胞移植后膈肌功能增强

Karim Azzag, Heather M Gransee, Alessandro Magli, Aline M S Yamashita, Sudheer Tungtur, Aaron Ahlquist, Wen-Zhi Zhan, Chiemelie Onyebu, Sarah M Greising, Carlos B Mantilla, Rita C R Perlingeiro

Establishment of Skeletal Myogenic Progenitors from Non-Human Primate Induced Pluripotent Stem Cells

从非人类灵长类动物诱导性多能干细胞建立骨骼肌祖细胞

June Baik, Carolina Ortiz-Cordero, Alessandro Magli, Karim Azzag, Sarah B Crist, Aline Yamashita, James Kiley, Sridhar Selvaraj, Ricardo Mondragon-Gonzalez, Elizabeth Perrin, John P Maufort, Jody L Janecek, Rachael M Lee, Laura Hocum Stone, Parthasarathy Rangarajan, Sabarinathan Ramachandran, Melani

Transplantation of PSC-derived myogenic progenitors counteracts disease phenotypes in FSHD mice

移植 PSC 衍生的成肌祖细胞可抵消 FSHD 小鼠的疾病表型

Karim Azzag, Darko Bosnakovski, Sudheer Tungtur, Peter Salama, Michael Kyba, Rita C R Perlingeiro

Fukutin-Related Protein: From Pathology to Treatments

福库汀相关蛋白:从病理学到治疗

Ortiz-Cordero, Carolina; Azzag, Karim; Perlingeiro, Rita C R