日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Progress on cell therapy for skeletal muscle disorders

骨骼肌疾病细胞疗法的进展

Azzag, Karim; Perlingeiro, Rita C R

Necessity of Notch3 signaling in myofiber maturation in a pluripotent stem cell transplant model.

在多能干细胞移植模型中,Notch3信号传导对肌纤维成熟是必需的。

Yamashita Aline M S, Crist Sarah B, Garay Bayardo I, Kim Hyunkee, Azzag Karim, Bosnakovski Darko, Faria Sergio H D M, Abrahante Juan E, Abreu Phablo, Ahlquist Aaron, Perlingeiro Rita C R

Preclinical quality, safety, and efficacy of a CGMP iPSC-derived myogenic progenitor product for the treatment of muscular dystrophies.

用于治疗肌营养不良症的 CGMP iPSC 衍生肌源性祖细胞产品的临床前质量、安全性和有效性

Azzag Karim, Magli Alessandro, Kiley James, Sumstad Darin, Kadidlo Diane, Crist Sarah B, Norris Beverly, Ahlquist Aaron, Hocum Stone Laura L, Everett John, Shappa Faustich Jill, Seelig Davis, Rangarajan Parthasarathy, Kim Hyunkee, Flory Craig, Bushman Frederic, Ramachandran Sabarinathan, Kang Peter B, Schumacher Robert J, Wagner John E, Kyba Michael, Graham Melanie L, McKenna David H, Perlingeiro Rita C R

Fukutin-Related Protein: From Pathology to Treatments

福库汀相关蛋白:从病理学到治疗

Ortiz-Cordero, Carolina; Azzag, Karim; Perlingeiro, Rita C R

In vitro expanded skeletal myogenic progenitors from pluripotent stem cell-derived teratomas have high engraftment capacity

体外扩增的源自多能干细胞衍生畸胎瘤的骨骼肌祖细胞具有很高的移植能力。

Xie, Ning; Chu, Sabrina N; Azzag, Karim; Schultz, Cassandra B; Peifer, Lindsay N; Kyba, Michael; Perlingeiro, Rita C R; Chan, Sunny S K

Crystal-like order and defects in metazoan epithelia with spherical geometry

具有球形几何结构的后生动物上皮细胞中晶体状有序结构和缺陷

Roshal, Daria S; Azzag, Karim; Le Goff, Emilie; Rochal, Sergei B; Baghdiguian, Stephen

Transplantation studies reveal internuclear transfer of toxic RNA in engrafted muscles of myotonic dystrophy 1 mice

移植研究揭示了强直性肌营养不良1型小鼠移植肌肉中毒性RNA的核间转移。

Mondragon-Gonzalez, Ricardo; Azzag, Karim; Selvaraj, Sridhar; Yamamoto, Ami; Perlingeiro, Rita C R

Pluripotent stem cell-derived myogenic progenitors remodel their molecular signature upon in vivo engraftment

多能干细胞衍生的成肌祖细胞在体内移植后会重塑其分子特征

Incitti, Tania; Magli, Alessandro; Darabi, Radbod; Yuan, Ce; Lin, Karena; Arpke, Robert W; Azzag, Karim; Yamamoto, Ami; Stewart, Ron; Thomson, James A; Kyba, Michael; Perlingeiro, Rita C R

CBP and P300 regulate distinct gene networks required for human primary myoblast differentiation and muscle integrity

CBP 和 P300 调控着不同的基因网络,这些网络对于人类原代成肌细胞分化和肌肉完整性至关重要。

Fauquier, Lucas; Azzag, Karim; Parra, Marco Antonio Mendoza; Quillien, Aurélie; Boulet, Manon; Diouf, Sarah; Carnac, Gilles; Waltzer, Lucas; Gronemeyer, Hinrich; Vandel, Laurence

The non-proliferative nature of ascidian folliculogenesis as a model of highly ordered cellular topology distinct from proliferative epithelia.

海鞘卵泡发生的非增殖特性,是高度有序的细胞拓扑结构的典型模型,与增殖性上皮截然不同

Azzag Karim, Chelin Yoann, Rousset François, Le Goff Emilie, Martinand-Mari Camille, Martinez Anne-Marie, Maurin Bernard, Daujat-Chavanieu Martine, Godefroy Nelly, Averseng Julien, Mangeat Paul, Baghdiguian Stephen