日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Author Correction: Fc-engineered large molecules targeting blood-brain barrier transferrin receptor and CD98hc have distinct central nervous system and peripheral biodistribution

作者更正:靶向血脑屏障转铁蛋白受体和CD98hc的Fc工程化大分子具有不同的中枢神经系统和外周生物分布。

Khoury, Nathalie; Pizzo, Michelle E; Discenza, Claire B; Joy, David; Tatarakis, David; Todorov, Mihail Ivilinov; Negwer, Moritz; Ha, Connie; De Melo, Gabrielly L; Sarrafha, Lily; Simon, Matthew J; Chan, Darren; Chau, Roni; Chew, Kylie S; Chow, Johann; Clemens, Allisa; Robles-Colmenares, Yaneth; Dugas, Jason C; Duque, Joseph; Kaltenecker, Doris; Kane, Holly; Leung, Amy; Lozano, Edwin; Moshkforoush, Arash; Roche, Elysia; Sandmann, Thomas; Tong, Mabel; Xa, Kaitlin; Zhou, Yinhan; Lewcock, Joseph W; Ertürk, Ali; Thorne, Robert G; Calvert, Meredith E K; Yu Zuchero, Y Joy

ABI5-binding proteins are substrates of key components in the ABA core signaling pathway affecting seeds.

ABI5 结合蛋白是影响种子的 ABA 核心信号通路中关键成分的底物。

Lynch Tim J, Erickson McNally B Joy, Losic Teodora, Lindquist Jonas, Finkelstein Ruth

Safety and efficacy of long-term gantenerumab treatment in dominantly inherited Alzheimer's disease: an open-label extension of the phase 2/3 multicentre, randomised, double-blind, placebo-controlled platform DIAN-TU trial

长期使用gantenerumab治疗显性遗传性阿尔茨海默病的安全性和有效性:一项2/3期多中心、随机、双盲、安慰剂对照平台DIAN-TU试验的开放标签扩展研究

Bateman, Randall J; Li, Yan; McDade, Eric M; Llibre-Guerra, Jorge J; Clifford, David B; Atri, Alireza; Mills, Susan L; Santacruz, Anna M; Wang, Guoqiao; Supnet, Charlene; Benzinger, Tammie L S; Gordon, Brian A; Ibanez, Laura; Klein, Gregory; Baudler, Monika; Doody, Rachelle S; Delmar, Paul; Kerchner, Geoffrey A; Bittner, Tobias; Wojtowicz, Jakub; Bonni, Azad; Fontoura, Paulo; Hofmann, Carsten; Kulic, Luka; Hassenstab, Jason; Aschenbrenner, Andrew J; Perrin, Richard J; Cruchaga, Carlos; Renton, Alan E; Xiong, Chengjie; Goate, Alison A; Morris, John C; Holtzman, David M; Snider, B Joy; Mummery, Catherine; Brooks, William S; Wallon, David; Berman, Sarah B; Roberson, Erik; Masters, Colin L; Galasko, Douglas R; Jayadev, Suman; Sanchez-Valle, Rachel; Pariente, Jeremie; Kinsella, Justin; van Dyck, Christopher H; Gauthier, Serge; Hsiung, Ging-Yuek Robin; Masellis, Mario; Dubois, Bruno; Honig, Lawrence S; Jack, Clifford R; Daniels, Alisha; Aguillón, David; Allegri, Ricardo; Chhatwal, Jasmeer; Day, Gregory; Fox, Nick C; Huey, Edward; Ikeuchi, Takeshi; Jucker, Mathias; Lee, Jae-Hong; Levey, Allan I; Levin, Johannes; Lopera, Francisco; Roh, JeeHoon; Rosa-Neto, Pedro; Schofield, Peter R

Lecanemab Treatment in a Specialty Memory Clinic

在专业记忆诊所接受Lecanemab治疗

Paczynski, Madeline; Hofmann, Anna; Posey, Zachary; Gregersen, Maren; Rudman, Michelle; Ellington, Dawn; Aldinger, Melissa; Musiek, Erik S; Holtzman, David M; Bateman, Randall J; Long, Justin M; Ghoshal, Nupur; Carr, David B; Dow, Alan; Namazie-Kummer, Sheyda; Jana, Nayid; Xiong, Chengjie; Morris, John C; Benzinger, Tammie L S; Schindler, Suzanne E; Snider, B Joy

A differentiated β-globin gene replacement strategy uses heterologous introns to restore physiological expression.

差异化的β-珠蛋白基因替换策略利用异源内含子来恢复生理表达

Wallace Kirby A, Gerstenberg Trevor L, Ennis Craig L, Perez-Bermejo Juan A, Partridge James R, Bandoro Christopher, Matern William M, Andreoletti Gaia, Krassovsky Kristina, Kabir Shaheen, Lalisan Cassandra D, Churi Aishwarya R, Chew Glen M, Corbo Lana, Vincelette Jon E, Klasson Timothy D, Silva Brian J, Strukov Yuri G, Quejarro B Joy, Hill Kaisle A, Treusch Sebastian, Grogan Jane L, Dever Daniel P, Porteus Matthew H, Wienert Beeke

Regional effects of gantenerumab on neuroimaging biomarkers in the DIAN-TU-001 trial

DIAN-TU-001试验中gantenerumab对神经影像学生物标志物的区域性影响

McCullough, Austin; Chen, Charles D; Gordon, Brian A; Joseph-Mathurin, Nelly; Jack, Clifford R Jr; Koeppe, Robert; Hornbeck, Russ; Koudelis, Deborah; McKay, Nicole S; Hobbs, Diana A; Flores, Shaney; Keefe, Sarah J; Aggarwal, Neelum T; Allegri, Ricardo F; Berman, Sarah B; Bird, Thomas; Black, Sandra E; Brooks, William S; Chhatwal, Jasmeer P; Day, Gregory S; Farlow, Martin R; Fox, Nick C; Gauthier, Serge; Honig, Lawrence S; Hsiung, Ging-Yuek; Jucker, Mathias; Levin, Johannes; Masellis, Mario; Masters, Colin; Mendez, Patricio Chrem; Ringman, John M; Snider, B Joy; Salloway, Stephen; Schofield, Peter R; Shimada, Hiroyuki; Suzuki, Kazushi; van Dyck, Christopher H; Klein, Gregory; Clifford, David B; Cruchaga, Carlos; Hassenstab, Jason; Li, Yan; McDade, Eric; Mills, Susan; Morris, John C; Perrin, Richard J; Supnet-Bell, Charlene; Wang, Guoqiao; Xiong, Chengjie; Bateman, Randall J; Benzinger, Tammie L S

System readiness and the patient care pathway for Alzheimer's disease diagnosis and treatment

系统准备情况以及阿尔茨海默病诊断和治疗的患者护理路径

Snider, B Joy; Biffi, Alessandro; Bozeat, Sasha; Clevenger, Carolyn; Farrar, Gill; Gitelman, Darren; Kolster, Rachel; Mattke, Soeren; Mielke, Michelle; Mukherjee, Debjani; Murphy, Jennifer; Okhravi, Hamid; Rabinovici, Gil D; Rentz, Dorene; Soria, Jose; Synder, Heather; Walker, Gregg; Mahinrad, Simin; Carrillo, Maria C; Weber, Christopher J

The Knight Alzheimer Research Imaging (KARI) dataset: a comprehensive multimodal resource for exploring aging, preclinical, and symptomatic Alzheimer disease pathology

Knight 阿尔茨海默病研究影像(KARI)数据集:用于探索衰老、临床前和症状性阿尔茨海默病病理的综合性多模态资源

Hoagey, David A; McKay, Nicole S; Joseph-Mathurin, Nelly; Flores, Shaney; Doering, Stephanie; Keefe, Sarah J; Hornbeck, Russ C; Smith, Thomas H; Scott, Jalen; Chen, Gengsheng; Massoumzadeh, Parinaz; LaMontagne, Pamela J; Wang, Qing; Hassenstab, Jason; Ponisio, Maria Rosana; Denny, Andrea; Balls-Berry, Joyce E; Snider, B Joy; Stark, Susan L; Xiong, Chengjie; Schindler, Suzanne E; Perrin, Richard J; Shimony, Joshua S; Goyal, Manu S; Vlassenko, Andrei G; Raichle, Marcus E; Morris, John C; Raji, Cyrus A; Gordon, Brian A; Benzinger, Tammie L S

Safety and efficacy of long-term gantenerumab treatment in dominantly inherited Alzheimer's disease: an open label extension of the phase 2/3 multicentre, randomised, double-blind, placebo-controlled platform DIAN-TU Trial

长期使用gantenerumab治疗显性遗传性阿尔茨海默病的安全性和有效性:一项开放标签扩展的2/3期多中心、随机、双盲、安慰剂对照平台DIAN-TU试验

Bateman, Randall J; Li, Yan; McDade, Eric M; Llibre-Guerra, Jorge J; Clifford, David B; Atri, Alireza; Mills, Susan L; Santacruz, Anna M; Wang, Guoqiao; Supnet, Charlene; Benzinger, Tammie L S; Gordon, Brian A; Ibanez, Laura; Klein, Gregory; Baudler, Monika; Doody, Rachelle S; Delmar, Paul; Kerchner, Geoffrey A; Bittner, Tobias; Wojtowicz, Jakub; Bonni, Azad; Fontoura, Paulo; Hofmann, Carsten; Kulic, Luka; Hassenstab, Jason; Aschenbrenner, Andrew J; Perrin, Richard J; Cruchaga, Carlos; Renton, Alan E; Xiong, Chengjie; Goate, Alison A; Morris, John C; Holtzman, David M; Snider, B Joy; Mummery, Catherine; Brooks, William S; Wallon, David; Berman, Sarah B; Roberson, Erik; Masters, Colin L; Galasko, Douglas R; Jayadev, Suman; Sanchez-Valle, Rachel; Pariente, Jeremie; Kinsella, Justin; van Dyck, Christopher H; Gauthier, Serge; Robin Hsiung, Ging-Yuek; Masellis, Mario; Dubois, Bruno; Honig, Lawrence S; Jack, Clifford R; Daniels, Alisha; Aguillón, David; Allegri, Ricardo; Chhatwal, Jasmeer; Day, Gregory; Fox, Nick; Huey, Edward; Ikeuchi, Takeshi; Jucker, Mathias; Lee, Jae-Hong; Levey, Allan I; Levin, Johannes; Lopera, Francisco; Roh, JeeHoon; Rosa-Neto, Pedro; Schofield, Peter R

Functional screening in human HSPCs identifies optimized protein-based enhancers of Homology Directed Repair

人类 HSPC 中的功能筛选可识别优化的基于蛋白质的同源定向修复增强子

Juan A Perez-Bermejo, Oghene Efagene, William M Matern, Jeffrey K Holden, Shaheen Kabir, Glen M Chew, Gaia Andreoletti, Eniola Catton, Craig L Ennis, Angelica Garcia, Trevor L Gerstenberg, Kaisle A Hill, Aayami Jain, Kristina Krassovsky, Cassandra D Lalisan, Daniel Lord, B Joy Quejarro, Jade Sales-L