Construction and validation of an RNA trans-splicing molecule suitable to repair a large number of COL7A1 mutations
适用于修复大量 COL7A1 突变的 RNA 反式剪接分子的构建和验证
期刊:Gene Therapy
影响因子:4.6
doi:10.1038/gt.2016.57
B Tockner, T Kocher, S Hainzl, J Reichelt, J W Bauer, U Koller, E M Murauer
