日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Preclinical safety and bleeding evaluation in swine for a small interfering RNA-lipid nanoparticle that prevents excess fibrinogen synthesis

在猪体内对一种可抑制纤维蛋白原过度合成的小干扰RNA-脂质纳米颗粒进行临床前安全性和出血性评估

Seadler, Monica S; Ferraresso, Francesca; Turner, Halen M; Ketelboeter, Laura M; Zhang, Youjie; Badior, Katherine; Hayssen, William G; Chen, Taylor; Haugen, Amber L; Cau, Massimo F; Robertson, Madelaine; Skaer, Chad; Bansal, Muskan; Murphy, Patrick B; de Moya, Marc; Dyer, Mitchell R; Kastrup, Christian J

Reversing PAI-1 deficiency in blood using mRNA lipid nanoparticles.

利用mRNA脂质纳米颗粒逆转血液中PAI-1缺乏症

Ferraresso Francesca, Skaer Chad W, Badior Katherine, Pulente Serena M, Paul Manoj, Ketelboeter Laura, Chen Taylor H S, Cullis Pieter R, Gupta Sweta, Shapiro Amy, Mulvihill Erin E, Kastrup Christian J

Protein is expressed in all major organs after intravenous infusion of mRNA-lipid nanoparticles in swine

猪静脉输注 mRNA-脂质纳米颗粒后,蛋白质在所有主要器官中表达

Francesca Ferraresso, Katherine Badior, Monica Seadler, Youjie Zhang, Amanda Wietrzny, Massimo F Cau, Amber Haugen, Geoffrey G Rodriguez, Mitchell R Dyer, Pieter R Cullis, Eric Jan, Christian J Kastrup

siRNA-mediated reduction of a circulating protein in swine using lipid nanoparticles

利用脂质纳米粒子通过 siRNA 介导减少猪体内的循环蛋白

Massimo F Cau, Francesca Ferraresso, Monica Seadler, Katherine Badior, Youjie Zhang, Laura M Ketelboeter, Geoffrey G Rodriguez, Taylor Chen, Matteo Ferraresso, Amanda Wietrzny, Madelaine Robertson, Amber Haugen, Pieter R Cullis, Marc de Moya, Mitchell Dyer, Christian J Kastrup

Genetically engineered transfusable platelets using mRNA lipid nanoparticles

利用mRNA脂质纳米颗粒的基因工程可输注血小板

Jerry Leung ,Colton Strong ,Katherine E Badior ,Madelaine Robertson ,Xiaowu Wu ,Michael A Meledeo ,Emma Kang ,Manoj Paul ,Yusuke Sato ,Hideyoshi Harashima ,Andrew P Cap ,Dana V Devine ,Eric Jan ,Pieter R Cullis ,Christian J Kastrup

Genetically engineered transfusable platelets using mRNA lipid nanoparticles

利用mRNA脂质纳米颗粒的基因工程可输注血小板

Jerry Leung ,Colton Strong ,Katherine E Badior,Madelaine Robertson ,Xiaowu Wu,Michael A Meledeo,Emma Kang,Manoj Paul,Yusuke Sato,Hideyoshi Harashima,Andrew P Cap,Dana V Devine ,Eric Jan,Pieter R Cullis,Christian J Kastrup          0