Mesenchymal stromal cell infusions of umbilical cord-derived mesenchymal stromal cells in children with recessive dystrophic epidermolysis bullosa (MissionEB): a randomised, double-blind, placebo controlled, crossover, phase 3 trial with an internal phase 1 dose de-escalation phase
脐带间充质干细胞输注治疗隐性营养不良型大疱性表皮松解症患儿（MissionEB）：一项随机、双盲、安慰剂对照、交叉设计的3期临床试验，并包含内部1期剂量递减阶段。
期刊:EClinicalMedicine
影响因子:10
doi:10.1016/j.eclinm.2025.103417
Bageta, Maria L; Lopez-Balboa, Pablo; Bursnall, Matt; Glover, Rachel; Hutchence, Kate; Papaioannou, Diana; Biggs, Katie; Julious, Steven; Wilson, Isabelle; Tappenden, Paul; Turton, Emily; Ditta, Shamila; Ogboli, Malobi; Lovgren, Marie-Louise; Poudel, Pratima; Nadeem, Muna; McGrath, John A; Cooper, Cindy; Petrof, Gabriela; Martinez, Anna E
