Long-Term Survival and Myocardial Function Following Systemic Delivery of Delandistrogene Moxeparvovec in DMD(MDX) Rats
在DMD(MDX)大鼠中全身给药Delandistrogene Moxeparvovec后的长期生存率和心肌功能
期刊:Human Gene Therapy
影响因子:4
doi:10.1089/hum.2024.013
Baine, Stephen; Wier, Chris; Lemmerman, Luke; Cooper-Olson, Grace; Kempton, Amber; Haile, Alex; Endres, Julian; Fedoce, Alessandra; Nesbit, Ellyn; Rodino-Klapac, Louise R; Potter, Rachael A