Death after High-Dose rAAV9 Gene Therapy in a Patient with Duchenne's Muscular Dystrophy
一名杜氏肌营养不良症患者接受高剂量rAAV9基因治疗后死亡
期刊:New England Journal of Medicine
影响因子:78.5
doi:10.1056/NEJMoa2307798
Lek, Angela; Wong, Brenda; Keeler, Allison; Blackwood, Meghan; Ma, Kaiyue; Huang, Shushu; Sylvia, Katelyn; Batista, A Rita; Artinian, Rebecca; Kokoski, Danielle; Parajuli, Shestruma; Putra, Juan; Carreon, C Katte; Lidov, Hart; Woodman, Keryn; Pajusalu, Sander; Spinazzola, Janelle M; Gallagher, Thomas; LaRovere, Joan; Balderson, Diane; Black, Lauren; Sutton, Keith; Horgan, Richard; Lek, Monkol; Flotte, Terence