P1405: IN-DEPTH GENOME INTEGRITY EVALUATION AND GMP-COMPLIANT MANUFACTURING OF HDR GENE EDITED CD4+ T CELLS FOR THE TREATMENT OF HYPER IGM 1
P1405:用于治疗高IgM 1 型免疫球蛋白血症的 HDR 基因编辑 CD4+ T 细胞的深入基因组完整性评估和符合 GMP 标准的生产
期刊:Nature Communications
影响因子:15.7
doi:10.1038/s41467-023-41038-7
García-López, Juan P; Grimaldi, Alexandre; Chen, Zelin; Meneses, Claudio; Bravo-Tello, Karina; Bresciani, Erica; Banderas, Alvaro; Burgess, Shawn M; Hernández, Pedro P; Feijoo, Carmen G; Maria Pinto, Valeria; Russo, Roberta; Quintino, Sabrina; Eleni Rosato, Barbara; Marra, Roberta; Del Giudice, Federica; Mogni, Massimo; Maffei, Massimo; Iolascon, Achille; Luca Forni, Gian; Andolfo, Immacolata; Canarutto, Daniele; Asperti, Claudia; Vavassori, Valentina; Porcellini, Simona; Rovelli, Elisabetta; Paulis, Marianna; Ferrari, Samuele; Plati, Tiziana; Sergi Sergi, Lucia; Villa, Anna; Radrizzani, Marina; Naldini, Luigi