日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Delivery of AAV vectors to the superior olivary complex enables efficient adult cochlear transduction via axonal transport

将腺相关病毒(AAV)载体递送至上橄榄复合体,可通过轴突运输实现高效的成人耳蜗转导。

Naidoo, Jerusha; Ren, Yin; Rocco, Matthew; Bielefeld, Eric; O'Brien, Allison; Kuo, Hsuan-Chih; McFarland, Nathan; Avenarius, Matthew; Takhar, Manpreet; Frank, Geneva; Van Laar, Victor; Bankiewicz, Krystof

Intraputaminal Delivery of Adeno-Associated Virus Serotype 2-Glial Cell Line-Derived Neurotrophic Factor in Mild or Moderate Parkinson's Disease

轻度或中度帕金森病患者壳核内注射腺相关病毒2型-胶质细胞系衍生神经营养因子

Van Laar, Amber D; Christine, Chadwick W; Phielipp, Nicolás; Larson, Paul S; Elder, J Bradley; Merola, Aristide; San Sebastian, Waldy; Fiandaca, Massimo S; Kells, Adrian P; Wisniewski, Michael E; Bankiewicz, Krystof S

A phase I study of convection-enhanced delivery (CED) of liposomal-irinotecan using real-time magnetic resonance imaging in patients with recurrent high-grade glioma

一项利用实时磁共振成像技术对复发性高级别胶质瘤患者进行脂质体伊立替康对流增强递送(CED)的I期研究

Narsinh, Kazim H; Kumar, Karishma; Bankiewicz, Krystof; Martin, Alastair J; Berger, Mitchell; Clarke, Jennifer; Taylor, Jennie; Bush, Nancy Ann Oberheim; Molinaro, Annette M; Aghi, Manish; Butowski, Nicholas

Efficient in vivo mammalian neuron editing using peptide-mediated CRISPR enzyme delivery

利用肽介导的CRISPR酶递送实现高效的体内哺乳动物神经元编辑

Manohar, Brigette D; Travis, Meika; Munjal, Vikas; Baehr, Christopher M; Rahnama, Lily M A; Kang, Min Hyung; Haddad, Rania F; Asija, Kunica; Noel, Eric A; Peddireddy, Navya; Chouhan, Runvir S; Sharma, Rohit; Wyman, Stacia K; Krishnappa, Netravathi; Killebrew, Deirdre A; Li, Song Hua; Snow, Kathy J; Byrne, Addison K; Boosani, Chandra S; Otero, P Anthony; Bringas, John; O'Brien, Allison A; Rocco, Matthew T; Zimmerly, Madison P; Gray, Isabelle; Sran, Gunita K; Patel, Mia I; Seidensticker, Emily F; Saville, Ethan; Gaitan, Yaned; Schmelzle, Amanda L; Subramanyam, Pradeep Nag B; Samaranch, Lluis; Green, Jonathan A; Wells, Kevin D; Ehrenberg, Alexander J; Murray, Stephen A; Clelland, Claire D; Murthy, Niren; Lonser, Russell R; Hadaczek, Piotr; Van Laar, Victor S; Bankiewicz, Krystof S; Wilson, Ross C

Persistent GDNF Expression 45 Months after Putaminal Infusion of AAV2-GDNF in a Patient with Parkinson's Disease

帕金森病患者壳核内注射AAV2-GDNF 45个月后,GDNF表达持续存在

Heiss, John D; Ray-Chaudhury, Abhik; Kleiner, David E; Ehrlich, Debra J; Scott, Gretchen; Edwards, Nancy A; Goldstein, David S; Hammoud, Dima A; Hadaczek, Piotr; Van Laar, Victor S; Graff, Shantelle A; Herscovitch, Peter; Lungu, Codrin; Hallett, Mark; Lonser, Russell R; Zaghloul, Kareem A; Bankiewicz, Krystof S

Validated assays for the quantification of C9orf72 human pathology

经过验证的定量 C9orf72 人类病理学检测方法

S E Salomonsson #, A M Maltos #, K Gill, O Aladesuyi Arogundade, K A Brown, A Sachdev, M Sckaff, K J K Lam, I J Fisher, R S Chouhan, V S Van Laar, C B Marley, I McLaughlin, K S Bankiewicz, Y-C Tsai, B R Conklin, C D Clelland

GDNF gene therapy for alcohol use disorder in male non-human primates

GDNF 基因治疗雄性非人类灵长类动物酒精使用障碍

Matthew M Ford #, Brianna E George #, Victor S Van Laar #, Katherine M Holleran #, Jerusha Naidoo, Piotr Hadaczek, Lauren E Vanderhooft, Emily G Peck, Monica H Dawes, Kousaku Ohno, John Bringas, Jodi L McBride, Lluis Samaranch, John R Forsayeth, Sara R Jones, Kathleen A Grant, Krystof S Bankiewicz

Targeting the IL4 receptor with MDNA55 in patients with recurrent glioblastoma: Results of a phase IIb trial

使用 MDNA55 靶向 IL4 受体治疗复发性胶质母细胞瘤患者:一项 IIb 期试验的结果

Sampson, John H; Singh Achrol, Achal; Aghi, Manish K; Bankiewicz, Krystof; Bexon, Martin; Brem, Steven; Brenner, Andrew; Chandhasin, Chandtip; Chowdhary, Sajeel; Coello, Melissa; Ellingson, Benjamin M; Floyd, John R; Han, Seunggu; Kesari, Santosh; Mardor, Yael; Merchant, Fahar; Merchant, Nina; Randazzo, Dina; Vogelbaum, Michael; Vrionis, Frank; Wembacher-Schroeder, Eva; Zabek, Miroslaw; Butowski, Nicholas

Safety of AADC Gene Therapy for Moderately Advanced Parkinson Disease: Three-Year Outcomes From the PD-1101 Trial

AADC基因疗法治疗中晚期帕金森病的安全性:PD-1101试验的三年结果

Christine, Chadwick W; Richardson, R Mark; Van Laar, Amber D; Thompson, Marin E; Fine, Elisabeth M; Khwaja, Omar S; Li, Chunming; Liang, Grace S; Meier, Andreas; Roberts, Eiry W; Pfau, Madeline L; Rodman, Josh R; Bankiewicz, Krystof S; Larson, Paul S

The NIH Somatic Cell Genome Editing program

美国国立卫生研究院体细胞基因组编辑计划

Saha, Krishanu; Sontheimer, Erik J; Brooks, P J; Dwinell, Melinda R; Gersbach, Charles A; Liu, David R; Murray, Stephen A; Tsai, Shengdar Q; Wilson, Ross C; Anderson, Daniel G; Asokan, Aravind; Banfield, Jillian F; Bankiewicz, Krystof S; Bao, Gang; Bulte, Jeff W M; Bursac, Nenad; Campbell, Jarryd M; Carlson, Daniel F; Chaikof, Elliot L; Chen, Zheng-Yi; Cheng, R Holland; Clark, Karl J; Curiel, David T; Dahlman, James E; Deverman, Benjamin E; Dickinson, Mary E; Doudna, Jennifer A; Ekker, Stephen C; Emborg, Marina E; Feng, Guoping; Freedman, Benjamin S; Gamm, David M; Gao, Guangping; Ghiran, Ionita C; Glazer, Peter M; Gong, Shaoqin; Heaney, Jason D; Hennebold, Jon D; Hinson, John T; Khvorova, Anastasia; Kiani, Samira; Lagor, William R; Lam, Kit S; Leong, Kam W; Levine, Jon E; Lewis, Jennifer A; Lutz, Cathleen M; Ly, Danith H; Maragh, Samantha; McCray, Paul B Jr; McDevitt, Todd C; Mirochnitchenko, Oleg; Morizane, Ryuji; Murthy, Niren; Prather, Randall S; Ronald, John A; Roy, Subhojit; Roy, Sushmita; Sabbisetti, Venkata; Saltzman, W Mark; Santangelo, Philip J; Segal, David J; Shimoyama, Mary; Skala, Melissa C; Tarantal, Alice F; Tilton, John C; Truskey, George A; Vandsburger, Moriel; Watts, Jonathan K; Wells, Kevin D; Wolfe, Scot A; Xu, Qiaobing; Xue, Wen; Yi, Guohua; Zhou, Jiangbing