日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Intraputaminal Delivery of Adeno-Associated Virus Serotype 2-Glial Cell Line-Derived Neurotrophic Factor in Mild or Moderate Parkinson's Disease

轻度或中度帕金森病患者壳核内注射腺相关病毒2型-胶质细胞系衍生神经营养因子

Van Laar, Amber D; Christine, Chadwick W; Phielipp, Nicolás; Larson, Paul S; Elder, J Bradley; Merola, Aristide; San Sebastian, Waldy; Fiandaca, Massimo S; Kells, Adrian P; Wisniewski, Michael E; Bankiewicz, Krystof S

Efficient in vivo mammalian neuron editing using peptide-mediated CRISPR enzyme delivery

利用肽介导的CRISPR酶递送实现高效的体内哺乳动物神经元编辑

Manohar, Brigette D; Travis, Meika; Munjal, Vikas; Baehr, Christopher M; Rahnama, Lily M A; Kang, Min Hyung; Haddad, Rania F; Asija, Kunica; Noel, Eric A; Peddireddy, Navya; Chouhan, Runvir S; Sharma, Rohit; Wyman, Stacia K; Krishnappa, Netravathi; Killebrew, Deirdre A; Li, Song Hua; Snow, Kathy J; Byrne, Addison K; Boosani, Chandra S; Otero, P Anthony; Bringas, John; O'Brien, Allison A; Rocco, Matthew T; Zimmerly, Madison P; Gray, Isabelle; Sran, Gunita K; Patel, Mia I; Seidensticker, Emily F; Saville, Ethan; Gaitan, Yaned; Schmelzle, Amanda L; Subramanyam, Pradeep Nag B; Samaranch, Lluis; Green, Jonathan A; Wells, Kevin D; Ehrenberg, Alexander J; Murray, Stephen A; Clelland, Claire D; Murthy, Niren; Lonser, Russell R; Hadaczek, Piotr; Van Laar, Victor S; Bankiewicz, Krystof S; Wilson, Ross C

Persistent GDNF Expression 45 Months after Putaminal Infusion of AAV2-GDNF in a Patient with Parkinson's Disease

帕金森病患者壳核内注射AAV2-GDNF 45个月后,GDNF表达持续存在

Heiss, John D; Ray-Chaudhury, Abhik; Kleiner, David E; Ehrlich, Debra J; Scott, Gretchen; Edwards, Nancy A; Goldstein, David S; Hammoud, Dima A; Hadaczek, Piotr; Van Laar, Victor S; Graff, Shantelle A; Herscovitch, Peter; Lungu, Codrin; Hallett, Mark; Lonser, Russell R; Zaghloul, Kareem A; Bankiewicz, Krystof S

Long-term safety of MRI-guided administration of AAV2-GDNF and gadoteridol in the putamen of individuals with Parkinson's disease

MRI引导下向帕金森病患者壳核内注射AAV2-GDNF和钆特醇的长期安全性

Rocco, Matthew T; Akhter, Asad S; Ehrlich, Debra J; Scott, Gretchen C; Lungu, Codrin; Munjal, Vikas; Aquino, Anthony; Lonser, Russell R; Fiandaca, Massimo S; Hallett, Mark; Heiss, John D; Bankiewicz, Krystof S

Safety of AADC Gene Therapy for Moderately Advanced Parkinson Disease: Three-Year Outcomes From the PD-1101 Trial

AADC基因疗法治疗中晚期帕金森病的安全性:PD-1101试验的三年结果

Christine, Chadwick W; Richardson, R Mark; Van Laar, Amber D; Thompson, Marin E; Fine, Elisabeth M; Khwaja, Omar S; Li, Chunming; Liang, Grace S; Meier, Andreas; Roberts, Eiry W; Pfau, Madeline L; Rodman, Josh R; Bankiewicz, Krystof S; Larson, Paul S

The NIH Somatic Cell Genome Editing program

美国国立卫生研究院体细胞基因组编辑计划

Saha, Krishanu; Sontheimer, Erik J; Brooks, P J; Dwinell, Melinda R; Gersbach, Charles A; Liu, David R; Murray, Stephen A; Tsai, Shengdar Q; Wilson, Ross C; Anderson, Daniel G; Asokan, Aravind; Banfield, Jillian F; Bankiewicz, Krystof S; Bao, Gang; Bulte, Jeff W M; Bursac, Nenad; Campbell, Jarryd M; Carlson, Daniel F; Chaikof, Elliot L; Chen, Zheng-Yi; Cheng, R Holland; Clark, Karl J; Curiel, David T; Dahlman, James E; Deverman, Benjamin E; Dickinson, Mary E; Doudna, Jennifer A; Ekker, Stephen C; Emborg, Marina E; Feng, Guoping; Freedman, Benjamin S; Gamm, David M; Gao, Guangping; Ghiran, Ionita C; Glazer, Peter M; Gong, Shaoqin; Heaney, Jason D; Hennebold, Jon D; Hinson, John T; Khvorova, Anastasia; Kiani, Samira; Lagor, William R; Lam, Kit S; Leong, Kam W; Levine, Jon E; Lewis, Jennifer A; Lutz, Cathleen M; Ly, Danith H; Maragh, Samantha; McCray, Paul B Jr; McDevitt, Todd C; Mirochnitchenko, Oleg; Morizane, Ryuji; Murthy, Niren; Prather, Randall S; Ronald, John A; Roy, Subhojit; Roy, Sushmita; Sabbisetti, Venkata; Saltzman, W Mark; Santangelo, Philip J; Segal, David J; Shimoyama, Mary; Skala, Melissa C; Tarantal, Alice F; Tilton, John C; Truskey, George A; Vandsburger, Moriel; Watts, Jonathan K; Wells, Kevin D; Wolfe, Scot A; Xu, Qiaobing; Xue, Wen; Yi, Guohua; Zhou, Jiangbing

Gene therapy for aromatic L-amino acid decarboxylase deficiency by MR-guided direct delivery of AAV2-AADC to midbrain dopaminergic neurons

利用磁共振引导将AAV2-AADC直接递送至中脑多巴胺能神经元,治疗芳香族L-氨基酸脱羧酶缺乏症的基因疗法

Pearson, Toni S; Gupta, Nalin; San Sebastian, Waldy; Imamura-Ching, Jill; Viehoever, Amy; Grijalvo-Perez, Ana; Fay, Alex J; Seth, Neha; Lundy, Shannon M; Seo, Youngho; Pampaloni, Miguel; Hyland, Keith; Smith, Erin; de Oliveira Barbosa, Gardenia; Heathcock, Jill C; Minnema, Amy; Lonser, Russell; Elder, J Bradley; Leonard, Jeffrey; Larson, Paul; Bankiewicz, Krystof S

An Update on Gene Therapy Approaches for Parkinson's Disease: Restoration of Dopaminergic Function

帕金森病基因治疗方法最新进展:多巴胺能功能的恢复

Van Laar, Amber D; Van Laar, Victor S; San Sebastian, Waldy; Merola, Aristide; Elder, J Bradley; Lonser, Russell R; Bankiewicz, Krystof S

Safety Assessment of AAV2-hGDNF Administered Via Intracerebral Injection in Rats for Treatment of Parkinson's Disease

大鼠脑内注射AAV2-hGDNF治疗帕金森病的安全性评估

Terse, Pramod S; Kells, Adrian P; Noker, Patricia; Wright, J Fraser; Bankiewicz, Krystof S

Development of a novel frameless skull-mounted ball-joint guide array for use in image-guided neurosurgery

开发一种新型的无框架颅骨安装式球形关节导向阵列,用于图像引导神经外科手术

Sudhakar, Vivek; Mahmoodi, Amin; Bringas, John R; Naidoo, Jerusha; Kells, Adrian; Samaranch, Lluis; Fiandaca, Massimo S; Bankiewicz, Krystof S