日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Liver-directed gene therapy for ornithine aminotransferase deficiency

肝脏定向基因治疗鸟氨酸转氨酶缺乏症

Iolanda Boffa, Elena Polishchuk, Lucia De Stefano, Fabio Dell'Aquila, Edoardo Nusco, Elena Marrocco, Matteo Audano, Silvia Pedretti, Marianna Caterino, Ilaria Bellezza, Margherita Ruoppolo, Nico Mitro, Barbara Cellini, Alberto Auricchio, Nicola Brunetti-Pierri

Dual species sphingosine-1-phosphate lyase inhibitors to combine antifungal and anti-inflammatory activities in cystic fibrosis: a feasibility study

双重鞘氨醇-1-磷酸裂解酶抑制剂联合使用在囊性纤维化中发挥抗真菌和抗炎作用:一项可行性研究

Barbara Cellini #, Gioena Pampalone #, Emidio Camaioni, Marilena Pariano, Flavia Catalano, Teresa Zelante, Mirco Dindo, Lara Macchioni, Alessandra Di Veroli, Roberta Galarini, Fabiola Paoletti, Magdalena Davidescu, Claudia Stincardini, Gianluca Vascelli, Marina Maria Bellet, Julie Saba, Stefano Giov

KIT 1 (Keep in Touch) Project-Televisits for Cancer Patients during Italian Lockdown for COVID-19 Pandemic: The Real-World Experience of Establishing a Telemedicine System

KIT 1(保持联系)项目——意大利新冠疫情封锁期间癌症患者的远程医疗:建立远程医疗系统的真实世界经验

Casà, Calogero; Corvari, Barbara; Cellini, Francesco; Cornacchione, Patrizia; D'Aviero, Andrea; Reina, Sara; Di Franco, Silvia; Salvati, Alessandra; Colloca, Giuseppe Ferdinando; Cesario, Alfredo; Patarnello, Stefano; Balducci, Mario; Morganti, Alessio Giuseppe; Valentini, Vincenzo; Gambacorta, Maria Antonietta; Tagliaferri, Luca

Identification of Human Alanine-Glyoxylate Aminotransferase Ligands as Pharmacological Chaperones for Variants Associated with Primary Hyperoxaluria Type 1

鉴定人类丙氨酸-乙醛酸氨基转移酶配体作为与原发性高草酸尿症 1 型相关的变异的药理学伴侣

Silvia Grottelli, Giannamaria Annunziato, Gioena Pampalone, Marco Pieroni, Mirco Dindo, Francesca Ferlenghi, Gabriele Costantino, Barbara Cellini

Structural dynamics shape the fitness window of alanine:glyoxylate aminotransferase

结构动力学塑造丙氨酸:乙醛酸氨基转移酶的适应窗口

Mirco Dindo, Stefano Pascarelli, Davide Chiasserini, Silvia Grottelli, Claudio Costantini, Gen-Ichiro Uechi, Giorgio Giardina, Paola Laurino, Barbara Cellini

MATRix-RICE therapy and autologous haematopoietic stem-cell transplantation in diffuse large B-cell lymphoma with secondary CNS involvement (MARIETTA): an international, single-arm, phase 2 trial

MATRix-RICE疗法联合自体造血干细胞移植治疗伴有中枢神经系统继发受累的弥漫性大B细胞淋巴瘤(MARIETTA):一项国际性、单臂、II期临床试验

Ferreri, Andrés J M; Doorduijn, Jeanette K; Re, Alessandro; Cabras, Maria Giuseppina; Smith, Jeffery; Ilariucci, Fiorella; Luppi, Mario; Calimeri, Teresa; Cattaneo, Chiara; Khwaja, Jahanzaib; Botto, Barbara; Cellini, Claudia; Nassi, Luca; Linton, Kim; McKay, Pam; Olivieri, Jacopo; Patti, Caterina; Re, Francesca; Fanni, Alessandro; Singh, Vikram; Bromberg, Jacoline E C; Cozens, Kelly; Gastaldi, Elisabetta; Bernardi, Massimo; Cascavilla, Nicola; Davies, Andrew; Fox, Christopher P; Frezzato, Maurizio; Osborne, Wendy; Liberati, Anna Marina; Novak, Urban; Zambello, Renato; Zucca, Emanuele; Cwynarski, Kate

Dimerization Drives Proper Folding of Human Alanine:Glyoxylate Aminotransferase But Is Dispensable for Peroxisomal Targeting

二聚化驱动人类丙氨酸:乙醛酸氨基转移酶的正确折叠,但对于过氧化物酶体靶向而言是可有可无的

Mirco Dindo, Giulia Ambrosini, Elisa Oppici, Angel L Pey, Peter J O'Toole, Joanne L Marrison, Ian E G Morrison, Elena Butturini, Silvia Grottelli, Claudio Costantini, Barbara Cellini

Mutant p53 proteins counteract autophagic mechanism sensitizing cancer cells to mTOR inhibition

突变的 p53 蛋白抵消了自噬机制,使癌细胞对 mTOR 抑制敏感

Marco Cordani, Elisa Oppici, Ilaria Dando, Elena Butturini, Elisa Dalla Pozza, Mercedes Nadal-Serrano, Jordi Oliver, Pilar Roca, Sofia Mariotto, Barbara Cellini, Giovanni Blandino, Marta Palmieri, Silvia Di Agostino, Massimo Donadelli

A Novel Pathway for Metabolism of the Cardiovascular Risk Factor Homoarginine by alanine:glyoxylate aminotransferase 2

心血管危险因素同型精氨酸通过丙氨酸:乙醛酸转氨酶 2 代谢的新途径

Roman N Rodionov, Elisa Oppici, Jens Martens-Lobenhoffer, Natalia Jarzebska, Silke Brilloff, Dmitrii Burdin, Anton Demyanov, Anne Kolouschek, James Leiper, Renke Maas, Barbara Cellini, Norbert Weiss, Stefanie M Bode-Böger