Intersecting impact of CAG repeat and huntingtin knockout in stem cell-derived cortical neurons.
CAG 重复序列和亨廷顿蛋白敲除对干细胞衍生皮层神经元的交叉影响。
期刊:Neurobiology of Disease
影响因子:5.6
doi:10.1016/j.nbd.2025.106914
Stocksdale Jennifer T, Leventhal Matthew J, Lam Stephanie, Xu Yu-Xin, Wang Yang Oliver, Wang Keona Q, Thomas Reuben, Faghihmonzavi Zohreh, Raghav Yogindra, Smith Charlene, Wu Jie, Miramontes Ricardo, Sarda Kanchan, Johnston Heather, Shin Min-Gyoung, Huang Terry, Foster Mikelle, Barch Mariya, Amirani Naufa, Paiz Chris, Easter Lindsay, Duderstadt Erse, Vaibhav Vineet, Sundararaman Niveda, Felsenfeld Dan P, Vogt Thomas F, Van Eyk Jennifer, Finkbeiner Steve, Kaye Julia A, Fraenkel Ernest, Thompson Leslie M