日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A 40-week phase 2B randomized, multicenter, double-blind, placebo-controlled study evaluating the safety and efficacy of memantine in amyotrophic lateral sclerosis

一项为期 40 周的 2B 期随机、多中心、双盲、安慰剂对照研究,旨在评估美金刚治疗肌萎缩侧索硬化症的安全性和有效性。

Bhai, Salman; Levine, Todd; Moore, Dan; Bowser, Robert; Heim, Andrew J; Walsh, Maureen; Shibani, Aziz; Simmons, Zachary; Grogan, James; Goyal, Namita A; Govindarajan, Raghav; Hussain, Yessar; Papsdorf, Tania; Schwasinger-Schmidt, Tiffany; Olney, Nick; Goslin, Kim; Pulley, Michael; Kasarskis, Edward; Weiss, Michael; Katz, Susan W; Moser, Suzan; Jabari, Duaa; Jawdat, Omar; Statland, Jeffrey; Dimachkie, Mazen M; Barohn, Richard

Resistance exercise in early-stage ALS patients, ALSFRS-R, Sickness Impact Profile ALS-19, and muscle transcriptome: a pilot study

早期肌萎缩侧索硬化症患者的抗阻运动、ALSFRS-R评分、疾病影响概况ALS-19评分和肌肉转录组:一项初步研究

Jawdat, Omar; Rucker, Jason; Nakano, Tomoki; Takeno, Kotaro; Statland, Jeffery; Pasnoor, Mamatha; Dimachkie, Mazen M; Sabus, Carla; Badawi, Yomna; Hunt, Suzanne L; Tomioka, Naoko H; Gunewardena, Sumedha; Bloomer, Clark; Wilkins, Heather M; Herbelin, Laura; Barohn, Richard J; Nishimune, Hiroshi

Longitudinal course of neurofilament light chain levels in amyotrophic lateral sclerosis-insights from a completed randomized controlled trial with rasagiline

肌萎缩侧索硬化症患者神经丝轻链水平的纵向变化——一项已完成的雷沙吉兰随机对照试验的启示

Witzel, Simon; Statland, Jeffrey M; Steinacker, Petra; Otto, Markus; Dorst, Johannes; Schuster, Joachim; Barohn, Richard J; Ludolph, Albert C

Conducting a bayesian multi-armed trial with response adaptive randomization for comparative effectiveness of medications for CSPN

开展一项贝叶斯多臂试验,采用响应自适应随机化方法,以比较药物治疗慢性周围神经病变(CSPN)的疗效。

Brown, Alexandra R; Gajewski, Byron J; Mudaranthakam, Dinesh Pal; Pasnoor, Mamatha; Dimachkie, Mazen M; Jawdat, Omar; Herbelin, Laura; Mayo, Matthew S; Barohn, Richard J

Effect of Different Corticosteroid Dosing Regimens on Clinical Outcomes in Boys With Duchenne Muscular Dystrophy: A Randomized Clinical Trial

不同皮质类固醇剂量方案对杜氏肌营养不良症男孩临床疗效的影响:一项随机临床试验

Guglieri, Michela; Bushby, Kate; McDermott, Michael P; Hart, Kimberly A; Tawil, Rabi; Martens, William B; Herr, Barbara E; McColl, Elaine; Speed, Chris; Wilkinson, Jennifer; Kirschner, Janbernd; King, Wendy M; Eagle, Michelle; Brown, Mary W; Willis, Tracey; Griggs, Robert C; Straub, Volker; van Ruiten, Henriette; Childs, Anne-Marie; Ciafaloni, Emma; Shieh, Perry B; Spinty, Stefan; Maggi, Lorenzo; Baranello, Giovanni; Butterfield, Russell J; Horrocks, I A; Roper, Helen; Alhaswani, Zoya; Flanigan, Kevin M; Kuntz, Nancy L; Manzur, Adnan; Darras, Basil T; Kang, Peter B; Morrison, Leslie; Krzesniak-Swinarska, Monika; Mah, Jean K; Mongini, Tiziana E; Ricci, Federica; von der Hagen, Maja; Finkel, Richard S; O'Reardon, Kathleen; Wicklund, Matthew; Kumar, Ashutosh; McDonald, Craig M; Han, Jay J; Joyce, Nanette; Henricson, Erik K; Schara-Schmidt, Ulrike; Gangfuss, Andrea; Wilichowski, Ekkehard; Barohn, Richard J; Statland, Jeffrey M; Campbell, Craig; Vita, Giuseppe; Vita, Gian Luca; Howard, James F Jr; Hughes, Imelda; McMillan, Hugh J; Pegoraro, Elena; Bello, Luca; Burnette, W Bryan; Thangarajh, Mathula; Chang, Taeun

Phase 2 Trial of Rituximab in Acetylcholine Receptor Antibody-Positive Generalized Myasthenia Gravis: The BeatMG Study

利妥昔单抗治疗乙酰胆碱受体抗体阳性全身型重症肌无力的 II 期临床试验:BeatMG 研究

Nowak, Richard J; Coffey, Christopher S; Goldstein, Jonathan M; Dimachkie, Mazen M; Benatar, Michael; Kissel, John T; Wolfe, Gil I; Burns, Ted M; Freimer, Miriam L; Nations, Sharon; Granit, Volkan; Smith, A Gordon; Richman, David P; Ciafaloni, Emma; Al-Lozi, Muhammad T; Sams, Laura Ann; Quan, Dianna; Ubogu, Eroboghene; Pearson, Brenda; Sharma, Aditi; Yankey, Jon W; Uribe, Liz; Shy, Michael; Amato, Anthony A; Conwit, Robin; O'Connor, Kevin C; Hafler, David A; Cudkowicz, Merit E; Barohn, Richard J

Pilot Study of Real-World Monitoring of the Heart Rate Variability in Amyotrophic Lateral Sclerosis

肌萎缩侧索硬化症患者心率变异性真实世界监测的试点研究

Brown, Alexander A; Ferguson, Bradley J; Jones, Vovanti; Green, Bruce E; Pearre, Justin D; Anunoby, Ifeoma A; Beversdorf, David Q; Barohn, Richard J; Cirstea, Carmen M

QOL-09. SyMon-SAYS: A symptom monitoring and reporting program for children with cancer

QOL-09. SyMon-SAYS:一项针对癌症患儿的症状监测和报告计划

Miller, Robert G; Zhang, Rongzhen; Bracci, Paige M; Azhir, Ari; Barohn, Richard; Bedlack, Richard; Benatar, Michael; Berry, James D; Cudkowicz, Merit; Kasarskis, Edward J; Mitsumoto, Hiroshi; Manousakis, Georgios; Walk, David; Oskarsson, Bjorn; Shefner, Jeremy; McGrath, Michael S; Malbari, Fatema; Erker, Craig; Driever, Pablo Hernáiz; Pillay-Smiley, Natasha; Avery, Robert A; Castellino, Robert Craig; Schouten-van Meeteren, Antoinette A Y N; Lenzen, Alicia C; Brandsma, Rick; Kramer, Kim; Baxter, Patricia A; Dhall, Girish; Goldman, Stewart; Wen, Patrick Y; Prados, Michael; Packer, Roger J; Warren, Katherine E; Nayak, Lakshmi; Marshall, Emily; Cheng, Sylvia; Crowley, Julia; McCormack, Shana; Rood, Brian; Hankinson, Todd; DeCuypere, Michael; Lam, Sandy; Goldman, Stewart; Boekhoff, Svenja; Muller, Hermann L; Velasco, Ryan; Storm, Phillip B; Resnick, Adam; Prados, Michael; Mueller, Sabine; Kline, Cassie; Malbari, Fatema; Lai, Jin-Shei; Jensen, Sally; Urban, Megan; Goldman, Stewart; Lenzen, Alicia

Patient Assisted Intervention for Neuropathy: Comparison of Treatment in Real Life Situations (PAIN-CONTRoLS): Bayesian Adaptive Comparative Effectiveness Randomized Trial

患者辅助干预治疗神经病变:真实情境下治疗的比较(疼痛控制):贝叶斯自适应比较效果随机试验

Barohn, Richard J; Gajewski, Byron; Pasnoor, Mamatha; Brown, Alexandra; Herbelin, Laura L; Kimminau, Kim S; Mudaranthakam, Dinesh Pal; Jawdat, Omar; Dimachkie, Mazen M; Iyadurai, Stanley; Stino, Amro; Kissel, John; Pascuzzi, Robert; Brannagan, Thomas; Wicklund, Matthew; Ahmed, Aiesha; Walk, David; Smith, Gordon; Quan, Dianna; Heitzman, Darryl; Tobon, Alejandro; Ladha, Shafeeq; Wolfe, Gil; Pulley, Michael; Hayat, Ghazala; Li, Yuebing; Thaisetthawatkul, Pariwat; Lewis, Richard; Biliciler, Suur; Sharma, Khema; Salajegheh, Kian; Trivedi, Jaya; Mallonee, William; Burns, Ted; Jacoby, Mark; Bril, Vera; Vu, Tuan; Ramchandren, Sindhu; Bazant, Mark; Austin, Sara; Karam, Chafic; Hussain, Yessar; Kutz, Christen; Twydell, Paul; Scelsa, Stephen; Kushlaf, Hani; Wymer, James; Hehir, Michael; Kolb, Noah; Ralph, Jeffrey; Barboi, Alexandru; Verma, Navin; Ahmed, Moiz; Memon, Anza; Saperstein, David; Lou, Jau-Shin; Swenson, Andrea; Cash, Tiyonnoh

Efficacy and Safety of Bimagrumab in Sporadic Inclusion Body Myositis: Long-term Extension of RESILIENT

Bimagrumab治疗散发性包涵体肌炎的疗效和安全性:RESILIENT研究的长期扩展

Amato, Anthony A; Hanna, Michael G; Machado, Pedro M; Badrising, Umesh A; Chinoy, Hector; Benveniste, Olivier; Karanam, Ananda Krishna; Wu, Min; Tankó, László B; Schubert-Tennigkeit, Agnes Annette; Papanicolaou, Dimitris A; Lloyd, Thomas E; Needham, Merrilee; Liang, Christina; Reardon, Katrina A; de Visser, Marianne; Ascherman, Dana P; Barohn, Richard J; Dimachkie, Mazen M; Miller, James A L; Kissel, John T; Oskarsson, Björn; Joyce, Nanette C; Van den Bergh, Peter; Baets, Jonathan; De Bleecker, Jan L; Karam, Chafic; David, William S; Mirabella, Massimiliano; Nations, Sharon P; Jung, Hans H; Pegoraro, Elena; Maggi, Lorenzo; Rodolico, Carmelo; Filosto, Massimiliano; Shaibani, Aziz I; Sivakumar, Kumaraswamy; Goyal, Namita A; Mori-Yoshimura, Madoka; Yamashita, Satoshi; Suzuki, Naoki; Aoki, Masashi; Katsuno, Masahisa; Morihata, Hirokazu; Murata, Kenya; Nodera, Hiroyuki; Nishino, Ichizo; Romano, Carla D; Williams, Valerie S L; Vissing, John; Zhang Auberson, Lixin