日期 影响因子
日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:
–

Systemic in utero gene editing as a treatment for cystic fibrosis

系统性子宫内基因编辑作为囊性纤维化的治疗方法

期刊:Proceedings of the National Academy of Sciences of the United States of America
影响因子:9.1
doi:10.1073/pnas.2418731122
Ricciardi, Adele S; Barone, Christina; Putman, Rachael; Quijano, Elias; Gupta, Anisha; Nguyen, Richard; Mandl, Hanna; Piotrowski-Daspit, Alexandra S; Lopez-Giraldez, Francesc; Luks, Valerie; Freedman-Weiss, Mollie R; Farrelly, James; Ahle, Samantha; Lynn, Anna Y; Glazer, Peter M; Saltzman, W Mark; Stitelman, David H; Egan, Marie E
发表日期：2025
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Next generation triplex-forming PNAs for site-specific genome editing of the F508del CFTR mutation

用于F508del CFTR突变位点特异性基因组编辑的新一代三链体形成PNA

期刊:Journal of Cystic Fibrosis
影响因子:6
doi:10.1016/j.jcf.2024.07.009
Gupta, Anisha; Barone, Christina; Quijano, Elias; Piotrowski-Daspit, Alexandra S; Perera, J Dinithi; Riccardi, Adele; Jamali, Haya; Turchick, Audrey; Zao, Weixi; Saltzman, W Mark; Glazer, Peter M; Egan, Marie E
CFTR
发表日期：2025
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In vivo correction of cystic fibrosis mediated by PNA nanoparticles

PNA纳米颗粒介导的囊性纤维化体内矫正

期刊:Science Advances
影响因子:12.5
doi:10.1126/sciadv.abo0522
Piotrowski-Daspit, Alexandra S; Barone, Christina; Lin, Chun-Yu; Deng, Yanxiang; Wu, Douglas; Binns, Thomas C; Xu, Emily; Ricciardi, Adele S; Putman, Rachael; Garrison, Alannah; Nguyen, Richard; Gupta, Anisha; Fan, Rong; Glazer, Peter M; Saltzman, W Mark; Egan, Marie E
发表日期：2022
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Loss of Cystic Fibrosis Transmembrane Regulator Impairs Intestinal Oxalate Secretion

囊性纤维化跨膜调节因子缺失会损害肠道草酸盐分泌

期刊:Journal of the American Society of Nephrology
影响因子:9.4
doi:10.1681/ASN.2016030279
Knauf, Felix; Thomson, Robert B; Heneghan, John F; Jiang, Zhirong; Adebamiro, Adedotun; Thomson, Claire L; Barone, Christina; Asplin, John R; Egan, Marie E; Alper, Seth L; Aronson, Peter S
发表日期：2017
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Increased susceptibility of Cftr-/- mice to LPS-induced lung remodeling.

Cftr-/- 小鼠对 LPS 诱导的肺重塑的易感性增加

期刊:American Journal of Physiology-Lung Cellular and Molecular Physiology
影响因子:3.5
doi:10.1152/ajplung.00284.2015
Bruscia Emanuela M, Zhang Ping-Xia, Barone Christina, Scholte Bob J, Homer Robert, Krause Diane S, Egan Marie E
发表日期：2016
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