日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Roads and detours for CAR T cell therapy in autoimmune diseases

CAR-T细胞疗法在自身免疫性疾病治疗中的道路和弯路

Avouac, Jérôme; Barzel, Adi; Caiati, Delma; Davis, Randall S; Gottschalk, Stephen; Grieshaber-Bouyer, Ricardo; Mao, Xuming; Luning Prak, Eline T; Radic, Marko; Scherlinger, Marc; Suneja, Yatin; Talleur, Aimee; Thacker, Amber L; Unutmaz, Derya

Mouse B cells engineered to express an anti-HPV antibody elicit anti-tumor T cell responses

经基因工程改造表达抗HPV抗体的鼠B细胞可诱导抗肿瘤T细胞反应。

Guberman Bracha, Michal; Biber, Guy; Zelikson, Natalie; Shavit, Sharon; Avraham, Roy; Vagima, Yaron; Bublik, Débora Rosa; Katz, Yael; Barzel, Adi; Klapper, Leah Natasha; Hess, Shmuel; Nahmad, Alessio David

Engineered human B cells targeting tumor-associated antigens exhibit antigen presentation and antibody-mediated functions.

针对肿瘤相关抗原的工程化人类B细胞表现出抗原呈递和抗体介导的功能

Boucher Alexander, Anderson Courtney, Hinman Rochelle, Kindschuh Molly, Fung Jeremy, Wang Tiansu, Klooster Isabella, Kim Elise, Roth Caroline, Vander Oever Michael, Khan Bakhmala, Zelikson Natalie, Vagima Yaron, Saribasak Huseyin, Santry Lisa, Klapper Leah Natasha, Hess Shmuel, Mooney Jill, Bublik Débora Rosa, Laken Haley, Barzel Adi, Borden Philip, Plewa Cherylene, Chadbourne Ana Maria, Bridgen Devin, Nahmad Alessio D

Correction: Expression of modified FcγRI enables myeloid cells to elicit robust tumor-specific cytotoxicity

更正:修饰型FcγRI的表达使髓系细胞能够引发强大的肿瘤特异性细胞毒性。

Farhat-Younis, Leen; Na, Manho; Zarfin, Amichai; Khateeb, Aseel; Santana-Magal, Nadine; Richter, Alon; Gutwillig, Amit; Rasoulouniriana, Diana; Gleiberman, Annette; Beck, Lir; Giger, Tamar; Ashkenazi, Avraham; Barzel, Adi; Rider, Peleg; Carmi, Yaron

MCP-1/CCR2 axis inhibition sensitizes the brain microenvironment against melanoma brain metastasis progression

MCP-1/CCR2轴抑制可增强脑微环境对黑色素瘤脑转移进展的敏感性

Pozzi, Sabina; Scomparin, Anna; Ben-Shushan, Dikla; Yeini, Eilam; Ofek, Paula; Nahmad, Alessio D; Soffer, Shelly; Ionescu, Ariel; Ruggiero, Antonella; Barzel, Adi; Brem, Henry; Hyde, Thomas M; Barshack, Iris; Sinha, Sanju; Ruppin, Eytan; Weiss, Tomer; Madi, Asaf; Perlson, Eran; Slutsky, Inna; Florindo, Helena F; Satchi-Fainaro, Ronit

Promoterless Gene Targeting Approach Combined to CRISPR/Cas9 Efficiently Corrects Hemophilia B Phenotype in Neonatal Mice

无启动子基因靶向方法结合 CRISPR/Cas9 技术可有效纠正新生小鼠的 B 型血友病表型

Lisjak, Michela; De Caneva, Alessia; Marais, Thibaut; Barbon, Elena; Biferi, Maria Grazia; Porro, Fabiola; Barzel, Adi; Zentilin, Lorena; Kay, Mark A; Mingozzi, Federico; Muro, Andrés F

Coupling AAV-mediated promoterless gene targeting to SaCas9 nuclease to efficiently correct liver metabolic diseases

将AAV介导的无启动子基因靶向与SaCas9核酸酶偶联,可有效纠正肝脏代谢疾病

De Caneva, Alessia; Porro, Fabiola; Bortolussi, Giulia; Sola, Riccardo; Lisjak, Michela; Barzel, Adi; Giacca, Mauro; Kay, Mark A; Vlahoviček, Kristian; Zentilin, Lorena; Muro, Andrés F

Promoterless gene targeting without nucleases rescues lethality of a Crigler-Najjar syndrome mouse model.

无需核酸酶的无启动子基因靶向可挽救克里格勒-纳贾尔综合征小鼠模型的致死性

Porro Fabiola, Bortolussi Giulia, Barzel Adi, De Caneva Alessia, Iaconcig Alessandra, Vodret Simone, Zentilin Lorena, Kay Mark A, Muro Andrés F