日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Development of an AAV-delivered microRNA gene therapy for myotonic dystrophy type 1

开发用于治疗1型强直性肌营养不良症的AAV递送microRNA基因疗法

Tomassy, Giulio S; Fan, Wei; Cao, Shuwen; Luo, Zhengyu; Magli, Alessandro; Zhang, Tracy; Boyle, Kristen; Jackson, Robert; Richards, Brenda; Liu, Dongyu; Rapaport, Franck; Khader, Shameer; Pfister, Edith L; O'Riordan, Catherine; Frederick, Amy; Sullivan, Jennifer; Cao, James; Nageswara Rao, Kollu; Assaf, Basel T; Goulet, Martin; Mueller, Christian

Nonclinical toxicity study duration in AAV gene therapy development: Evidence from industry survey supports adequacy of short-term assessments

AAV基因治疗研发中非临床毒性研究的持续时间:行业调查证据支持短期评估的充分性

Assaf, Basel T; Edwards, David; Berens, Shawn Jay; Lauritzen, Brian; Pierrot, Christelle; Tukov, Francis Fonyuy; Bertinetti-Lapatki, Cristina; Braun, Manuela; Schaefer, Kai; Lynch, Jessica L

KCNT1 (Slack/Slo2.2) and KCNT2 (Slick/Slo2.1) Dysregulation in Intellectual Disability and Behavioral Phenotypes: A Systematic Review

KCNT1 (Slack/Slo2.2) 和 KCNT2 (Slick/Slo2.1) 失调与智力障碍和行为表型:系统性综述

Murugesan, Karthika; Kabir, Areeba; Tomalieh, Basel T; Torres, Jessica; Kasagga, Alousious; Rebellow, Delvy

PET/CT vs PET/MRI in Lung Cancer: A Narrative Review of Diagnostic Performance, Practical Trade-offs, and Clinical Impact

PET/CT 与 PET/MRI 在肺癌诊断中的比较:诊断性能、实际权衡和临床影响的叙述性综述

Tomalieh, Basel T; Torres Luna, Jessica D; Murugesan, Karthika; Kabir, Areeba; Rebellow, Delvy; Kasagga, Alousious; Anwar, Summayya

AI in Digital Pathology for Diffuse Large B-cell Lymphoma: A Systematic Review of Diagnosis and Classification

人工智能在弥漫性大B细胞淋巴瘤数字病理学中的应用:诊断和分类的系统评价

Torres Luna, Jessica D; Tomalieh, Basel T; Rebellow, Delvy; Kasagga, Alousious; Kabir, Areeba; Murugesan, Karthika; Chavez Cavalie, Paolo S

In vivo overexpression of frataxin causes toxicity mediated by iron-sulfur cluster deficiency

体内 frataxin 过度表达导致由铁硫簇缺乏介导的毒性

Claudia Huichalaf, Tyler L Perfitt, Anna Kuperman, Renea Gooch, Ramesh C Kovi, Karrie A Brenneman, Xian Chen, Dinesh Hirenallur-Shanthappa, Tiffany Ma, Basel T Assaf, Ingrid Pardo, Tania Franks, Laura Monarski, Ting-Wen Cheng, Kevin Le, Chunyan Su, Suryanarayan Somanathan, Laurence O Whiteley, Chris

Embedded 3D Printing of Novel Bespoke Soft Dosage Form Concept for Pediatrics

新型定制软性药物制剂概念的嵌入式3D打印(适用于儿科)

Rycerz, Katarzyna; Stepien, Krzysztof Adam; Czapiewska, Marta; Arafat, Basel T; Habashy, Rober; Isreb, Abdullah; Peak, Matthew; Alhnan, Mohamed A

Limited dissemination and shedding of the UL128 complex-intact, UL/b'-defective rhesus cytomegalovirus strain 180.92

UL128复合物完整、UL/b'缺陷的恒河猴巨细胞病毒180.92株的传播和脱落有限

Assaf, Basel T; Mansfield, Keith G; Strelow, Lisa; Westmoreland, Susan V; Barry, Peter A; Kaur, Amitinder

A case of von Hippel-Lindau disease with exudative maculopathy

一例伴有渗出性黄斑病变的冯·希佩尔-林道病病例

Ba Arah, Basel T