Exploring Quality of Life in Adults Living With Late-onset Pompe Disease: A Combined Quantitative and Qualitative Analysis of Patient Perceptions from Australia, France, Italy, and the Netherlands
探索晚发型庞贝病成年患者的生活质量:来自澳大利亚、法国、意大利和荷兰的患者感知定量与定性相结合的分析
期刊:Journal of Health Economics and Outcomes Research
影响因子:2.3
doi:10.36469/001c.126018
Lumgair, Holly; Bashorum, Lisa; MacCulloch, Alasdair; Minas, Elizabeth; Timmins, George; Bratkovic, Drago; Perry, Richard; Stone, Medi; Blazos, Vasileios; Conti, Elisabetta; Saich, Raymond