日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A synthetic opsin restores vision in patients with severe retinal degeneration

一种合成视蛋白可以恢复严重视网膜变性患者的视力

Mohanty, Samarendra K; Mahapatra, Santosh; Batabyal, Subrata; Carlson, Michael; Kanungo, Gayatri; Ayyagari, Ananta; Tchedre, Kissaou; Franco, Joel A; Singer, Michael; Barone, Samuel B; Chavala, Sai; Mahajan, Vinit B

Response: Promise and open questions of optogenetic vision restoration by MCO

回复:MCO 的光遗传学视觉恢复技术展现出的前景和尚待解决的问题

Mohanty, Samarendra K; Mahapatra, Santosh; Batabyal, Subrata; Carlson, Michael; Kanungo, Gayatri; Ayyagari, Ananta; Tchedre, Kissaou; Franco, Joel A; Singer, Michael; Barone, Samuel; Chavala, Sai; Mahajan, Vinit B

Safety and efficacy of MCO-010 optogenetic therapy in patients with Stargardt disease in USA (STARLIGHT): an open-label multi-center Ph2 trial

MCO-010 光遗传疗法在美国治疗 Stargardt 病患者的安全性和有效性(STARLIGHT):一项开放标签、多中心 II 期临床试验

Lam, Byron L; Zak, Vitaliy; Gonzalez, Victor H; Gregori, Ninel Z; Chavala, Sai H; Batabyal, Subrata; Carlson, Michael; Kim, Sanghoon; Ayyagari, Ananta; Chang, Jean; Lane, Hayley; Choudry, Nozhat; Koester, John; Von Tress, Mark; Piltz-Seymour, Jody; Sharif, Najam A; Tsang, Stephen H; Mahajan, Vinit B; Boyer, David S; Ho, Allen C; Barone, Samuel B; Mohanty, Samarendra K

Engineered sensor actuator modulator as aqueous humor outflow actuator for gene therapy of primary open-angle glaucoma

用于原发性开角型青光眼基因治疗的工程化传感器执行器调节器作为房水流出执行器

Mohanty, Samarendra; Batabyal, Subrata; Idigo, Chinenye; Narcisse, Darryl; Kim, Sanghoon; Al-Saad, Houssam; Carlson, Michael; Tchedre, Kissaou; Dibas, Adnan

Sensitization of ON-bipolar cells with ambient light activatable multi-characteristic opsin rescues vision in mice

利用环境光激活的多特性视蛋白敏化ON型双极细胞可挽救小鼠的视力

Batabyal, Subrata; Gajjeraman, Sivakumar; Pradhan, Sanjay; Bhattacharya, Sulagna; Wright, Weldon; Mohanty, Samarendra

Bioluminescent Multi-Characteristic Opsin for Simultaneous Optical Stimulation and Continuous Monitoring of Cortical Activities

用于同时进行光刺激和连续监测皮层活动的生物发光多特性视蛋白

Narcisse, Darryl; Mustafi, Sourajit Mitra; Carlson, Michael; Batabyal, Subrata; Kim, Sanghoon; Wright, Weldon; Kumar Mohanty, Samarendra

Monitoring Visual Cortical Activities During Progressive Retinal Degeneration Using Functional Bioluminescence Imaging

利用功能性生物发光成像技术监测进行性视网膜变性过程中的视觉皮层活动

Narcisse, Darryl; Mustafi, Sourajit M; Carlson, Michael; Kim, Sanghoon; Batabyal, Subrata; Wright, Weldon; Mohanty, Samarendra K

Layer-specific nanophotonic delivery of therapeutic opsin-encoding genes into retina.

将治疗性视蛋白编码基因通过纳米光子技术定向递送至视网膜

Batabyal Subrata, Kim Sanghoon, Wright Weldon, Mohanty Samarendra

Restoring vision in mice with retinal degeneration using multicharacteristic opsin

利用多特征视蛋白恢复视网膜退化小鼠的视力

Wright, Weldon; Gajjeraman, Sivakumar; Batabyal, Subrata; Pradhan, Sanjay; Bhattacharya, Sulagna; Mahapatra, Vasu; Tripathy, Ashutosh; Mohanty, Samarendra

Erratum: Publisher's note: Restoring vision in mice with retinal degeneration using multicharacteristic opsin

勘误:出版商注:利用多特征视蛋白恢复视网膜退化小鼠的视力

Wright, Weldon; Gajjeraman, Sivakumar; Batabyal, Subrata; Pradhan, Sanjay; Bhattacharya, Sulagna; Mahapatra, Vasu; Tripathy, Ashutosh; Mohanty, Samarendra