日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Nucleotide-resolution mapping of regulatory elements via allelic readout of tiled base editing.

通过等位基因读取平铺碱基编辑,实现调控元件的核苷酸分辨率定位。

Becerra Basheer, Wittibschlager Sandra, Patel Zain M, Kutschat Ana P, Delano Justin, Che Eric, Tauber Anzhelika, Wu Ting, Starrs Marlena, Horstmann Christina S, Müller Sophie, Whittaker Madelynn N, Sylvander Elise, Lehner Manfred, Love Michael I, Kleinstiver Benjamin P, Jankowiak Martin, Bauer Daniel E, Seruggia Davide, Pinello Luca

Enhancing prime editing in hematopoietic stem and progenitor cells by modulating nucleotide metabolism

通过调节核苷酸代谢增强造血干细胞和祖细胞中的基因编辑

Levesque, Sébastien; Cosentino, Andrea; Verma, Archana; Genovese, Pietro; Bauer, Daniel E

In situ gene editing of hematopoietic stem cells via AAV-delivered CRISPR guide RNAs

利用腺相关病毒载体递送的CRISPR引导RNA对造血干细胞进行原位基因编辑

Karimzadeh, Alborz; Kim, Rebekah; Garcia, Vivian; Florea, Michael; Peacker, Bryan L; Kobayashi, Shio; Watkins, Drake; Messemer, Kathleen; Zeng, Jing; Bauer, Daniel E; Serwold, Thomas; Wagers, Amy J

A xeno-free red blood cell differentiation formula models sickle cell disease from somatically sourced patient iPSCs

一种不含异种成分的红细胞分化配方,利用体细胞来源的患者诱导多能干细胞(iPSCs)模拟镰状细胞病。

Conway, Ashlee J; Rosanwo, Tolulope O; Williamson, Thomas E; Landry, Samuel; Kinney, Melissa A; Clark, Martha A; Vo, Linda T; Rowe, R Grant; Marion, William; Zhang, Yosra; Mullin, Nathaniel K; Shi, Michael; Archer, Natasha M; Heeney, Matthew M; Schlaeger, Thorsten M; Bauer, Daniel E; Duraisingh, Manoj T; Brugnara, Carlo; North, Trista E; Daley, George Q

Analyzing long-read CRISPR experiments with CRISPRLungo

使用 CRISPRLungo 分析长读长 CRISPR 实验

Hwang, Gue-Ho; Vyshedskiy, Benjamin; Barry, Timothy; Zeng, Jing; Manis, John P; Shimamura, Akiko; Bauer, Daniel E; Pinello, Luca

In cellulo DNA assembly for targeted genomic integration and rearrangement in human cells

在人类细胞中进行细胞内DNA组装,以实现靶向基因组整合和重排

Levesque, Sébastien; Kawashima, Nozomu; Hwang, GueHo; Becerra, Basheer; Schoonenberg, Vivien A C; Mannherz, William; Homfeldt, Luke; Pinello, Luca; Agarwal, Suneet; Bauer, Daniel E

Direct and indirect regulation of fetal globin transcript by RNA-binding protein IGF2BP1

RNA结合蛋白IGF2BP1对胎儿珠蛋白转录的直接和间接调控

Coyne, Steven; Wu, Ting; Hossain, Mir; Vinjamur, Divya; Starrs, Marlena; Zeng, Jing; Andresen, Felicia; Gutierrez, Ashley; Shimamura, Akiko; Bauer, Daniel E

Modular platform for therapeutic drug delivery using trifunctional bio-orthogonal macromolecular conjugates

利用三功能生物正交大分子缀合物进行治疗药物递送的模块化平台

Luo, Danmeng; Wang, Ning; Major-Monfried, Hannah; Ralls, John; Rha, Sophia; Maitland, Stacy A; Ponnienselvan, Karthikeyan; Yamada, Makiko; Bauer, Daniel E; Wolfe, Scot A; Kentsis, Alex

A viable alternative for editor delivery

编辑交付的可行替代方案

Eweje, Feyisayo; Bauer, Daniel E

Assessing and advancing the safety of CRISPR-Cas tools: from DNA to RNA editing

评估和提升 CRISPR-Cas 工具的安全性:从 DNA 编辑到 RNA 编辑

Tao, Jianli; Bauer, Daniel E; Chiarle, Roberto