日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Author Correction: The type II RAF inhibitor tovorafenib in relapsed/refractory pediatric low-grade glioma: the phase 2 FIREFLY-1 trial

作者更正:II型RAF抑制剂托沃拉非尼治疗复发/难治性儿童低级别胶质瘤:II期FIREFLY-1试验

Kilburn, Lindsay B; Khuong-Quang, Dong-Anh; Hansford, Jordan R; Landi, Daniel; van der Lugt, Jasper; Leary, Sarah E S; Driever, Pablo Hernáiz; Bailey, Simon; Perreault, Sébastien; McCowage, Geoffrey; Waanders, Angela J; Ziegler, David S; Witt, Olaf; Baxter, Patricia A; Kang, Hyoung Jin; Hassall, Timothy E; Han, Jung Woo; Hargrave, Darren; Franson, Andrea T; Yalon Oren, Michal; Toledano, Helen; Larouche, Valérie; Kline, Cassie; Abdelbaki, Mohamed S; Jabado, Nada; Gottardo, Nicholas G; Gerber, Nicolas U; Whipple, Nicholas S; Segal, Devorah; Chi, Susan N; Oren, Liat; Tan, Enrica E K; Mueller, Sabine; Cornelio, Izzy; McLeod, Lisa; Zhao, Xin; Walter, Ashley; Da Costa, Daniel; Manley, Peter; Blackman, Samuel C; Packer, Roger J; Nysom, Karsten

Radiographic and visual response to the type II RAF inhibitor tovorafenib in children with relapsed/refractory optic pathway glioma in the FIREFLY-1 trial

FIREFLY-1试验中,复发/难治性视路胶质瘤患儿对II型RAF抑制剂托沃拉非尼的放射学和视觉反应

Nysom, Karsten; Kilburn, Lindsay B; Leary, Sarah E S; Landi, Daniel B; de Vos-Kerkhof, Evelien; Perreault, Sébastien; Witt, Olaf; Ziegler, David S; Hernáiz Driever, Pablo; Franson, Andrea T; Baxter, Patricia A; Whipple, Nicholas S; Kline, Cassie; Segal, Devorah; Jabado, Nada; Bailey, Simon; McCowage, Geoffrey; Hansford, Jordan R; Khuong-Quang, Dong-Anh; Gottardo, Nicholas G; Hassall, Timothy; Han, Jung Woo; Yalon Oren, Michal; Chi, Susan N; Qiu, Jiaheng; Da Costa, Daniel; Govinda Raju, Sandya; Manley, Peter; Hargrave, Darren

Phase 2 trial of veliparib, local irradiation, and temozolomide in patients with newly diagnosed high-grade glioma: a Children's Oncology Group study

儿童肿瘤协作组开展的一项针对新诊断高级别胶质瘤患者的维利帕尼、局部放疗和替莫唑胺联合治疗的II期临床试验研究

Karajannis, Matthias A; Onar-Thomas, Arzu; Lin, Tong; Baxter, Patricia A; Boué, Daniel R; Cole, Bonnie L; Fuller, Christine; Haque, Sofia; Jabado, Nada; Lucas, John T Jr; MacDonald, Shannon M; Matsushima, Celeste; Patel, Namrata; Pierson, Christopher R; Souweidane, Mark M; Thomas, Diana L; Walsh, Michael F; Zaky, Wafik; Leary, Sarah E S; Gajjar, Amar; Fouladi, Maryam; Cohen, Kenneth J

The type II RAF inhibitor tovorafenib in relapsed/refractory pediatric low-grade glioma: the phase 2 FIREFLY-1 trial

II 型 RAF 抑制剂托沃拉非尼治疗复发/难治性儿童低级别胶质瘤:II 期 FIREFLY-1 试验

Kilburn, Lindsay B; Khuong-Quang, Dong-Anh; Hansford, Jordan R; Landi, Daniel; van der Lugt, Jasper; Leary, Sarah E S; Driever, Pablo Hernáiz; Bailey, Simon; Perreault, Sébastien; McCowage, Geoffrey; Waanders, Angela J; Ziegler, David S; Witt, Olaf; Baxter, Patricia A; Kang, Hyoung Jin; Hassall, Timothy E; Han, Jung Woo; Hargrave, Darren; Franson, Andrea T; Yalon Oren, Michal; Toledano, Helen; Larouche, Valérie; Kline, Cassie; Abdelbaki, Mohamed S; Jabado, Nada; Gottardo, Nicholas G; Gerber, Nicolas U; Whipple, Nicholas S; Segal, Devorah; Chi, Susan N; Oren, Liat; Tan, Enrica E K; Mueller, Sabine; Cornelio, Izzy; McLeod, Lisa; Zhao, Xin; Walter, Ashley; Da Costa, Daniel; Manley, Peter; Blackman, Samuel C; Packer, Roger J; Nysom, Karsten

CTNI-09. TYPE II RAF INHIBITOR TOVORAFENIB IN RELAPSED/REFRACTORY (R/R) PEDIATRIC LOW-GRADE GLIOMA (PLGG): RESULTS FROM PATIENTS ON A DRUG HOLIDAY (DH) IN THE PHASE 2 FIREFLY-1 TRIAL

CTNI-09. II型RAF抑制剂托沃拉非尼治疗复发/难治性(R/R)儿童低级别胶质瘤(PLGG):FIREFLY-1 II期试验中停药(DH)患者的结果

Veiga, Luís D; Teixeira, Inês F; Vaz, Joana B; Leite, Paula; Gonçalves, Joana; Perreault, Sébastien; Khuong-Quang, Dong-Anh; Kilburn, Lindsay B; Landi, Daniel B; Leary, Sarah E S; Bailey, Simon; Larouche, Valérie; Nysom, Karsten; Driever, Pablo Hernáiz; Baxter, Patricia A; Witt, Olaf; Oren, Michal Yalon; Abdelbaki, Mohamed S; Kline, Cassie; Whipple, Nicholas S; Ziegler, David S; van der Lugt, Jasper; Hassall, Timothy E; Gerber, Nicolas U; Segal, Devorah; Hansford, Jordan R; McCowage, Geoffrey; Kang, Hyoung Jin; Han, Jung Woo; Hargrave, Darren; Franson, Andrea T; Toledano, Helen; Jabado, Nada; Gottardo, Nicholas G; Chi, Susan N; Oren, Liat; Tan, Enrica E K; Mueller, Sabine; Hoke, Molly E; Kim, Yeonhee; Walter, Ashley; Da Costa, Daniel; Manley, Peter; Waanders, Angela J

EPID-01. ESTIMATING THE BURDEN DUE TO BRAIN AND OTHER CNS TUMORS IN ADOLESCENTS IN THE UNITED STATES

EPID-01. 估算美国青少年脑肿瘤和其他中枢神经系统肿瘤造成的疾病负担

Soleimani, Najme; Iraji, Armin; van Erp, Theo G M; Belger, Aysenil; Calhoun, Vince D; Kline, Cassie; Franson, Andrea; Banerjee, Anuradha; Reddy, Alyssa T; Raber, Shannon; Hoffman, Carly; Minturn, Jane; van der Lugt, Jasper; de Vos-Kerkhof, Evelien; van Vuurden, Dannis; Gerber, Nicolas; Stucklin, Ana S Guerreiro; Kilburn, Lindsay; Elster, Jennifer; Whipple, Nicholas; Cohen, Kenneth; Oren, Michal Yalon; Gardner, Sharon; Cluster, Andrew; Chi, Susan; Landi, Daniel; McCowage, Geoffrey; Vo, Josh; Resnick, Adam; Phillips, Joanna; Bhatia, Aashim; George, Elizabeth; Vossough, Arastoo; Nabavizadeh, Ali; Braunstein, Steve; Gupta, Nalin; Prados, Michael; Waszak, Sebastian; Long-Boyle, Janel; Molinaro, Annette; Dun, Matthew; Koschmann, Carl; Nazarian, Javad; Mueller, Sabine; Lange, Katharine R; deBlank, Peter; Xing, Mengqi; Mirzaei, Sedigheh; Srivastava, Deo Kumar; Oeffinger, Kevin; Neglia, Joseph; Krull, Kevin; Nathan, Paul; Howell, Rebecca; Ness, Kirsten K; Turcotte, Lucie; Leisenring, Wendy; Armstrong, Gregory T; Brinkman, Tara; Bowers, Daniel C; Okcu, M Fatih; Wright-Nadkarni, Mariah L; Moscato, Emily L; Stanek, Joseph R; Schaefer, Megan R; Gerhardt, Cynthia A; Ashley, David M; Baxter, Patricia A; Chi, Susan N; Dorris, Kathleen; Fisher, Michael J; Hummel, Trent R; Hwang, Eugene I; Gass, David; Leary, Sarah E S; Pillay-Smiley, Natasha; Plant, Ashley S; Murala, Mythili; Mikael, Leonie; Fouladi, Maryam; Lazow, Margot A; Dhall, Girish; Stanek, Joseph; Blue, Megan; Patel, Parth; Thomas, Diana; Pierson, CHristopher; Tamrazi, Benita; Mahadeo, Kris; Fleming, Jessica; Bell, Erica; MIller, Katherine; Grischow, Olivia; Liszkay, Thomas; Owen, Scott; Hastings, Caroline; Tsui, Karen; Mazewski, Claire; Friedman, Gregory; Moertel, Christopher; Hanson, Derek; Koschman, Carl; Brock, Guy; Asgharzadeh, Shahab; Chakravarti, Arnab; Wong, Kenneth; Nelson, Marvin; Boue, Daniel; Biegel, Jaclyn; Mardis, Elaine; Finlay, Jonathan; Galvin, Robert T; Sadeghipour, Negar; Xiu, Joanne; Ashley, David M; Ahluwalia, Manmeet S; Aulakh, Sonikpreet; Huang, R Stephanie; Largaespada, David A; Avery, Robert; Jiang, Zhifan; Parida, Abhijeet; Listernick, Robert; Liu, Grant; Ferner, Rosalie; Gutmann, David; de Blank, Peter; Lasky-Zeid, Janice; Ullrich, Nicole; Heidary, Gena; Bornhorst, Miriam; Stasheff, Steven; Rosser, Teena; Borchert, Mark; Arden-Holmes, Simone; Flaherty, Maree; Hummel, Trent; Motley, Walker; Bielamowicz, Kevin; Phillips, Paul; Bouffet, Eric; Reginald, Arun; Wolf, David; Peragallo, Jason; Van Mater, David; El-Diari, Mays; Sato, Aimee; Tarczy-Hornoch, Kristina; Klesse, Laura; Hogan, Nick; Foreman, Nicholas; McCourt, Emily; Allen, Jeffrey; Ranka, Milan; Campen, Cynthia; Beres, Shannon; Moertel, Christopher; Areaux, Ray; Stearns, Duncan; Orge, Faruk; Crawford, John; O’Halloran, Henry; Brodsky, Michael; Esbenshade, Adam; Donahue, Sean; Oattes, Julius; Reddy, Alyssa; Cutter, Gary; Linguraru, Marius; Fisher, Michael; Gajjar, Amar J; Orr, Brent; Ellison, David; Lafay-Cousin, Lucie; Minturn, Jane; Fisher, Michael; Bendel, Anne; Hwang, Eugene; Murray, Jeffrey; Landi, Daniel; Smith, Amy; Gottardo, Nicholas; Valvi, Santhosh; Hassal, Tim; Elster, Jennifer; Perrault, Sebastian; Ramaswamy, Vijay; Partap, Sonia; Laughton, Stephen; Cohn, Richard; Chintagumpala, Murali; McCowage, Geoffrey; Hansford, Jordan; Sullivan, Michael; Sayour, Elias; Bowers, Daniel; Marks, Asher; Huang, Jie; Lucas, John; Tinkle, Christopher; Pinto, Soniya; Bag, Asim; Sabin, Noah; Northcott, Paul; Klimo, Paul; Merchant, Thomas E; Onar-Thomas, Arzu; Robinson, Giles W; Price, Mackenzie; Neff, Corey; Kruchko, Carol; Waite, Kristin A; Cioffi, Gino; Cordeiro, Brittany; Penas-Prado, Marta; Gilbert, Mark R; Armstrong, Terri S; Barnholtz-Sloan, Jill S; Ostrom, Quinn T

NFS-03. MEDULLOBLASTOMA IN CHILDREN WITH FANCONI ANEMIA: ASSOCIATION WITH FA-D1/FA-N, SHH TYPE AND POOR SURVIVAL INDEPENDENT OF TREATMENT STRATEGIES

NFS-03. 范可尼贫血患儿髓母细胞瘤:与 FA-D1/FA-N、SHH 型及与治疗策略无关的低生存率相关

Chukwu, Wolu; Lee, Siyun; Crane, Alexander; Zhang, Shu; Webster, Sophie; Mittra, Ipsa; Imielinski, Marcin; Beroukhim, Rameen; Dubois, Frank; Dalin, Simona; Seelow, Dominik; Öz, Elif; Hardt, Annika; Kortmann, Rolf-Dieter; Schwarz, Rudolf; Timmermann, Beate; Bison, Brigitte; Warmuth-Metz, Monika; von Hoff, Katja; von Bueren, André O; Gerber, Nicolas U; Fleischhack, Gudrun; Pietsch, Torsten; Pfister, Stefan M; Sturm, Dominik; Mynarek, Martin; Rutkowski, Stefan; Obrecht-Sturm, Denise; Faria Andrade*, Augusto; Sigaud*, Romain; Puligandla*, Evan; Liu, Bridget; Karimi, Elham; Schmid, Simone; Selt, Florian; Driever, Pablo Hernáiz; Koch, Arend; Sahm, Felix; Sievers, Philipp; Pfister, Stefan M; Witt, Olaf; Jones, David T W; Capper, David; Walsh*, Logan; Jabado*, Nada; Milde*, Till; Ghasemi, David R; von Hoff, Katja; Obrecht-Sturm, Denise; Wenning, Janna; Mynarek, Martin; Gerber, Nicolas U; Benesch, Martin; Juhnke, Björn O; Bison, Brigitte; Warmuth-Metz, Monika; Timmermann, Beate; Faldum, Andreas; Fleischhack, Gudrun; Grotzer, Michael; Driever, Pablo Hernáiz; Beilken, Andreas; Ebinger, Martin; Graf, Norbert; Frühwald, Michael; Schmid, Irene; Koch, Arend; Bergmann, Markus; Hagel, Christian; Coras, Roland; Blümcke, Ingmar; Reifenberger, Guido; Felsberg, Jörg; Keyvani, Kathy; Harter, Patrick N; Prinz, Marco; Staszewski, Ori; Acker, Till; Brück, Wolfgang; Hartmann, Christian; von Deimling, Andreas; Sommer, Clemens; Hasselblatt, Martin; Riemenschneider, Markus J; Monoranu, Camelia-Maria; Rushing, Elisabeth; Kool, Marcel; Pfister, Stefan M; Schüller, Ulrich; Pietsch, Torsten; Kortmann, Rolf D; Kwiecien, Robert; Witt, Hendrik; Pajtler, Kristian W; Rutkowski, Stefan; Fruehwald, Michael C; Boros, Matej; Dahlum, Sonja; Bens, Susanne; Johann, Pascal D; Kachanov, Denis; Hauser, Peter; Kratz, Christian P; Hernaiz-Driever, Pablo; Eyrich, Matthias; Sumerauer, David; Milde, Till; Reinhard, Harald; van de Wetering, Marianne; Gil-da-Costa, Maria Joao; Elisabetta, Schiavello; Kerl, Kornelius; Furtwaengler, Rhoikos; Kordes, Uwe; Gerss, Joachim; Hasselblatt, Martin; Nysom, Karsten; Nemes, Karolina; Kline, Cassie; Waanders, Angela J; Ziegler, David S; Kilburn, Lindsay B; Nysom, Karsten; van der Lugt, Jasper; Hassall, Timothy E; Gerber, Nicolas U; Segal, Devorah; Larouche, Valérie; Khuong-Quang, Dong-Anh; Hansford, Jordan R; Leary, Sarah E S; Driever, Pablo Hernáiz; Bailey, Simon; Perreault, Sébastien; McCowage, Geoffrey; Witt, Olaf; Baxter, Patricia A; Kang, Hyoung Jin; Han, Jung Woo; Hargrave, Darren; Franson, Andrea T; Oren, Michal Yalon; Toledano, Helen; Abdelbaki, Mohamed S; Jabado, Nada; Gottardo, Nicholas G; Whipple, Nicholas S; Chi, Susan N; Oren, Liat; Tan, Enrica E K; Mueller, Sabine; Wright, Karen D; Blackman, Samuel C; Qiu, Jiaheng; Podesta, Dolores; Walter, Ashley; Da Costa, Daniel; Manley, Peter; McLeod, Lisa; Landi, Daniel B; Geisemeyer, Neal; Federico, Aniello; Sill, Martin; Rosenblum, Marc; Bale, Tejus; Mauermann, Monika; Schrimpf, Daniel; Johann, Pascal; Pickles, Jessica; Aldape, Kenneth; Tauziède-Espariat, Arnault; Hasselblatt, Martin; Sturm, Dominik; Tietze, Anna; von Deimling, Andreas; Sievers, Philipp; Sahm, Felix; Gojo, Johannes; von Hoff, Katja; Pfister, Stefan M; Kool, Marcel; Keck, Michaela-Kristina; Tietze, Anna; Sievers, Philipp; Bison, Brigitte; Avula, Shivaram; Brandner, Sebastian; Cheesman, Edmund; Faure-Conter, Cécile; Fenouil, Tanguy; Figarella-Branger, Dominique; Gauchotte, Guillaume; Goebell, Einar; Gojo, Johannes; Haberler, Christine; Hakumäki, Juhana; Hayden, James T; Jabado, Nada; Korhonen, Laura S; Korshunov, Andrey; Koscielniak, Ewa; Kramm, Christof M; Kranendonk, Mariëtte E G; Lavarino, Cinzia; Lequin, Maarten; Loiseau, Hugues; Ludlow, Louise E; Maher, Ossama; Meyronet, David; Nyman, Per; Øra, Ingrid; Perwein, Thomas; Pesola, Jouni; Rauramaa, Tuomas; Reddingius, Roel; Samuel, David; Schouten-van Meeteren, Antoinette Y N; Schüller, Ulrich; Sexton-Oates, Alexandra; Solomon, David; Varlet, Pascale; Vasiljevic, Alexandre; von Kalle, Thekla; Wefers, Annika K; Wesseling, Pieter; White, Christine; Zamecnik, Josef; Zapotocky, Michal; von Hoff*, Katja; Jones*, David T W; Stepien, Natalia; Senfter, Daniel; Freund, Julia; Machreich, Sarah; Bruckner, Katharina; Mager, Leah; Laemmerer, Anna; Jaunecker, Carola; Pirker, Christine; Lötsch-Gojo, Daniela; Mayr, Lisa; Hedrich, Cora; Lippolis, Maria Aliotti; Schned, Hannah; Köller, Clara; Kiesel, Barbara; Dorfer, Christian; Azizi, Amedeo A; Peyrl, Andreas; Schmook, Maria T; Euskirchen, Philipp; Pagès-Gallego, Marc; Vermeulen, Carlo; Tops, Bastiaan; Haberler, Christine; Müllauer, Leonhard; Madlener, Sibylle; Gojo, Johannes; Schned, Hannah; Haberler, Christine; Peyrl, Andreas; Azizi, Amedeo; Mayr, Lisa; Aistleitner, Barbara; von Hoff, Katja; Kool, Marcel; Kjaersgaard, Mimi; Trkova, Katerina; Andre, Nicolas; Lippolis, Maria Aliotti; Hedrich, Cora; Köller, Clara; Stepien, Natalia; Slavc, Irene; Gojo, Johannes; Traunwieser, Thomas; Loos, Elena; Ottensmeier, Holger; Mynarek, Martin; Bison, Brigitte; Kandels, Daniela; Rossius, Anne; Lüttich, Peggy; Baust, Katja; Faulstich-Ritter, Kristin; John, Rainer; Kreisch, Andrea; Landmann, Judyta; Manteufel, Eva; Nest, Alexandra; Prüfe, Jenny; Schubert, Lisa; Stamm, Walther; Timmermann, Beate; Gerss, Joachim; Rutkowski, Stefan; Schlegel, Paul-Gerhardt; Eyrich, Matthias; Gnekow, Astrid K; Frühwald, Michael C; Sönksen, Marthe; Obrecht-Sturm, Denise; Driever, Pablo Hernáiz; Sauerbrey, Axel; Graf, Norbert; Kontny, Udo; Reimann, Christian; Kordes, Uwe; Schwarz, Rudolf; Obser, Tobias; Boschann, Felix; Schüller, Ulrich; Altendorf, Lea; Goschzik, Tobias; Pietsch, Torsten; Mynarek, Martin; Rutkowski, Stefan

LINC-14. A single center retrospective analysis of pediatric pineoblastoma in Beijing

LINC-14. 北京地区儿童松果体母细胞瘤单中心回顾性分析

Ventz, Steffen; Comment, Leah; Louv, Bill; Rahman, Rifaquat; Wen, Patrick Y; Alexander, Brian M; Trippa, Lorenzo; Pillay Smiley, Natasha; Leach, James; Lane, Adam; Hummel, Trent; Fangusaro, Jason; de Blank, Peter; Messiaen, Julie; Antoranz, Asier; Van Herck, Yannick; Verhaaren, Ben; Nazari, Pouya; Sebastian, Ivey; Milli, Giorgia; Bosisio, Francesca; Pey, Jon; Bempt, Isabelle Vanden; Sciot, Raf; Jacobs, Sandra; De Smet, Frederik; Lamola, Lindiwe; Manolas, Erin; Krause, Amanda; Wang, Dong; Veo, Bethany; Pierce, Angela; Venkataraman, Sujatha; Vibhakar, Rajeev; Chan, Priya; Sabus, Ashley; Hemenway, Molly; Chatfield, Kathryn; Foreman, Nicholas; Dahl, Nathan; Gorodezki, David; Sosa, Jordana; Holzer, Ursula; Queudeville, Manon; Zipfel, Julian; Bevot, Andrea; Schittenhelm, Jens; Nägele, Thomas; Ebinger, Martin; Schuhmann, Martin; Mack, Stephen; Cantor, Evan; Meyer, Ashley; Ogle, Andrea; McHugh, Michele; Beck, Mary; Green, Tammy; Ramachandran, Lakshmi; Dahiya, Sonika; Cluster, Andrew; Brossier, Nicole M; Abdelbaki, Mohamed S; Limbrick, David; Perkins, Stephanie; Shatara, Margaret; Eisemann, Tanja; Wechsler-Reya, Robert; Maass, Kendra K; Roosen, Mieke M; Mueller, Torsten; Senfter, Daniel; Benzel, Julia; Wedig, Tatjana; Kalxsdorf, Mathias; Krijgsveld, Jeroen; Pfister, Stefan M; Pajtler, Kristian W; Perek-Polnik, Marta; Cochrane, Anne; Chojnacka, M; Drogosiewicz, M; Filipek, I; Swieszkowska, E; Tarasinska, M; Kowalczyk, P; Abdelbaki, Mohamed S; Dembowska-Bagińska, Bożenna; Jaunecker, Carola N; Kirchhofer, Dominik; Madlener, Sibylle; Laemmerer, Anna; Gabler, Lisa; Pirker, Christine; Piontek, Martin; Maaß, Kendra; Okonechnikov, Konstanitin; Englinger, Bernhard; Jiang, Li; Mayr, Lisa; Senfter, Daniel; Spiegl-Kreinecker, Sabine; Stepien, Natalia; Dorfer, Christian; Filbin, Mariella; Kool, Marcel; Gojo, Johannes; Berger, Walter; Loetsch-Gojo, Daniela; Tonn, Svenja; Obrecht, Denise; Sill, Martin; Spohn, Michael; Milde, Till; Pietsch, Torsten; Bison, Brigitte; Juhnke, Björn-Ole; Struve, Nina; Friedrich, Carsten; von Bueren, André O; Gerber, Nicolas U; Benesch, Martin; Jäger, Natalie; Kool, Marcel; Korshunov, Andrey; Schüller, Ulrich; Pfister, Stefan M; Rutkowski, Stefan; Mynarek, Martin; Mobark, Nahla Ali; Alharbi, Musa; Ballourah, Walid; AlSultan, Abdulrahman; Manjomi, Fahad Al; Alotabi, Fahad; Balbaid, Ali Abdullah O; Rayis, Mohammed; AlNaqib, Zaid G; Aljabarat, Wael abdel Rahman; Finlay, Jonathan L; Pletschko, Thomas; Pelzer, Clarissa; Röhsner, Martin; Rockenbauer, Gerda; Turner, Agnes; Gudenas, Brian; Englinger, Bernhard; Liu, Anthony P Y; Ahmad, Sheikh Tanveer; Meredith, David; Pfaff, Elke; Paul, Leena; Hadley, Jennifer; Batts, Melissa; Klimo, Paul Jr; Boop, Frederick A; Gajjar, Amar; Robinson, Giles; Orr, Brent; Lin, Hong; Alexandrescu, Sanda; Jones, David T W; Filbin, Mariella G; Northcott, Paul A; Tang, Phua Hwee; Nisa, Sameema; Barreto, Juliana Silveira; Gomez, Karen Nirit Melo; Dutra, Alvaro Pimenta; De Azambuja, Alessandra Milani Prandini; Cristofani, Lilian Maria; Sanders, Felipe Hada; Petito, Carlo; Baraldi, Helena Espindola; Weltman, Eduardo; Ferraciolli, Suely Fazio; Frassetto, Fernando Pereira; Lucato, Leandro Tavares; Rosemberg, Sérgio; Filho, Vicente Odone; de Faria, Flavia W; Walter, Carolin; Interlandi, Marta; Melcher, Viktoria; Riedel, Nicole; Graf, Monika; Moreno, Natalia; Schoof, Melanie; Holdhof, Dörthe; Thomas, Christian; Frühwald, Michael C; Maerkl, Bruno; Ho, Ben; Sandmann, Sarah; Varghese, Julian; Ebinger, Martin; Schuhmann, Martin; Canak, Aysegül; Huang, Annie; Schüller, Ulrich; Albert, Thomas K; Kerl, Kornelius; Hegde, Kriti; Dahl, Christine; Depani, Sarita; Hargrave, Darren; Oostveen, Minou; Aguirregomezcorta, Fernando; Jeelani, Owase; Aquilina, Kristian; Gains, Jenny; Ching, Yen; Jacues, Thomas; Merve, Ashirwad; Chalker, Jane; Addy, Dilys; Ahmed, Saira W; Yasin, Shireen; Mankad, Kshitij; Carney, Olivia; Sudhakar, Sniya; D'Arco, Felice; Loebel, Ulrike; Jorgensen, Mette; Swiderska-Syn, Marzena; Mir-Pedrol, Julia; Rodriguez-Blanco, Jezabel; Nobre, Liana; Johnson, Monique; Siddaway, Robert; Sheth, Javal; Ryall, Scott; Ku, Michelle; Lyn, Rodney; Stucklin, Ana; Zapotocky, Michal; Tabori, Uri; Hawkins, Cynthia; Abdelmoula, Balkiss; Abid, Fatma; Karra, Amir; Kammoun, Sonda; Aloulou, Samir; Abdelmoula, Nouha Bouayed; Goddard, Jack; Castle, Jemma; Southworth, Emily; Fletcher, Anya; Crosier, Stephen; Martin-Guerrero, Idoia; Garcia-Ariza, Miguel; Navajas, Aurora; Masliah-Planchon, Julien; Bourdeaut, Franck; Dufour, Christelle; Goschizk, Tobias; Pietsch, Torsten; Richardson, Stacey; Hill, Rebecca M; Williamson, Daniel; Bailey, Simon; Schwalbe, Edward C; Clifford, Steven C; Hicks, Debbie; Sesen, Julie; Ghalali, Aram; Martinez, Tyra; Driscoll, Jessica; Fehnel, Katie Pricola; Smith, Edward; Apps, John; Pickles, Jessica; Stone, Thomas; Chalker, Jane; Ogunbiyi, Olumide; Schwalbe, Edward; Brandner, Sebastian; Otto, Georg; Castellano, Sergi; Jacques, Thomas; Deutschbein, Timo; Martinez-Barbera, Juan Pedro; Piatelli, Gianluca; Pavanello, Marco; Piccolo, Gianluca; Rossi, Andrea; Garrè, Maria Luisa; De Marco, Patrizia; Iurilli, Valentina; Antonelli, Manila; Gaggero, Gabriele; Caruggi, Samuele; Verrico, Antonio; Crocco, Marco; Milanaccio, Claudia; Mishra, Deepak; Wang, Jie; Chen, Chun-Yu; Zhu, Xiaoting; Kumar, Shiva Senthil; McHugh, Todd; Cripe, Timothy; Fouladi, Maryam; Drissi, Rachid; Hardin, Emily C; Schmid, Simone; Sommerkamp, Alexander; le Simon, Michè; Caspar, Claudia; Bodden, Carina; Heipertz, Anna-Elisa; Sievers, Philipp; Wittmann, Andrea; Perera, Ashwyn A; Milde, Till; Pfister, Stefan M; von Deimling, Andreas; Driever, Pablo Hernáiz; Koch, Arend; Hargrave, Darren; Witt, Olaf; Capper, David; Sahm, Felix; Jones, David T W; van Tilburg, Cornelis M; Chapman, Owen; Sridhar, Sunita; Wechsler-Reya, Robert J; Chavez, Lukas; Mesirov, Jill P; Hotblack, Alastair; Wawrzyniecka, Patrycja; Cheng, Gordon Weng-Kit; Nannini, Francesco; Pule, Martin; Straathof, Karin; Guadix, Sergio; de Silva, Neranjan; Souweidane, Mark; Riley, Kathy; Fitzgerald, Caroline; Matson, Kathryn; Li, Miao; Du, Shuxu; Tian, Yongji; Zhang, Jin; Gao, Wenchao; Xiao, Jinjing; Gong, Xiaojun; Sun, Yanling; Wu, Wanshui; Sun, Liming; Madhavan, Krishna; Balakrishnan, Ilango; Lakshmanachetty, Senthilnath; Pierce, Angela; Sanford, Bridget; Fosmire, Susan; Elajaili, Hanan; Walker, Faye; Wang, Dong; Nozik-Grayck, Eva; Mitra, Siddhartha; Dahl, Nathan; Vibhakar, Rajeev; Venkataraman, Sujatha; Chatterjee, Jit; Sanapala, Shilpa; Cobb, Olivia; Bewley, Alice; Cordell, Elizabeth; Garbow, Joel; Holtzman, Michael; Gutmann, David; Zou, Han; Poore, Bradley; Brown, Emily; Hu, Zhongliang; Li, Xuejun; Pollack, Ian; Friedlander, Robert; Hainer, Sarah; Taylor, Michael; Hu, Baoli; Entwistle, Susannah; Jackson, Hannah K; Kerr, Ian; Coyle, Beth; Hume, Alistair; Singh, Pankaj; Chandra, Sarat; Kale, Shashank; Lupien, Leslie; Rendo, Veronica; Morin, Eric; Khuu, Nicholas; DiGiacomo, Jeromy; Khadka, Prasidda; Chacon, Madison; Lu, Sophie; Pelton, Kristine; Elcavage, Lara; Langhnoja, Jaldeep; Ligon, Keith; Beroukhim, Rameen; Phoenix, Timothy; Bandopadhayay, Pratiti; Orduña, Patricia; Lubaton-Sacro, Cheryl Anne; Rechberger, Julian; Porath, Kendra; Schrecengost, Randy; Sarkaria, Jann; Daniels, David; Nazarian, Javad; Dun, Matthew; Kilburn, Lindsay; Waszak, Sebastian; Vitanza, Nicholas; Franson, Andrea; Prados, Mike; Raabe, Eric; Firestein, Ron; Beck, Alexander; Saratsis, Amanda; Rotblat, Barak; van Vuurder, Dannis; Foster, Jessica; Hulleman, Esther; Kline, Cassie; Gupta, Nalin; Cain, Jason; Koschmann, Carl; Muller, Sabine; Li, Miao; Du, Shuxu; Sun, Yanling; Gong, Xiaojun; Liu, Jingjing; Ren, Siqi; Zhang, Jin; Gao, Wenchao; Li, Shuting; Wan, Lulu; Wang, Yuan; Wu, Yuefang; Liu, Yan; Zhang, Zhen; Tang, Hong; Wu, Wanshui; Sun, Liming; Raju, Praveen; Tylawsky, Daniel; Vaynshteyn, Jake; Gerwin, Jeffrey; Heller, Daniel; Snuderl, Matija; Baudou, Eloïse; Pollidoro, Lisa; Tallet, Jessica; Danna, Jérémy; Pariente, Jérémie; Chaix, Yves; Laprie, Anne; Crotty, Erin; Cole, Bonnie; Stasi, Shannon; Vitanza, Nicholas; Paulson, Vera; Lockwood, Christina; Leary, Sarah; Ku, Dennis T L; Liu, Anthony P Y; Kan, Amanda N C; Yuen, Liz Y P; Shing, M K; Yan, Carol Y L; Fu, Eric; Yau, Jeffrey P W; Luk, C W; Ng, H K; Chan, Godfrey C F; Malbari, Fatema; Erker, Craig; Driever, Pablo Hernáiz; Pillay-Smiley, Natasha; Avery, Robert A; Castellino, Robert Craig; Schouten-van Meeteren, Antoinette A Y N; Lenzen, Alicia C; Brandsma, Rick; Kramer, Kim; Baxter, Patricia A; Dhall, Girish; Goldman, Stewart; Wen, Patrick Y; Prados, Michael; Packer, Roger J; Warren, Katherine E; Nayak, Lakshmi; Lobon-Iglesias, Maria; Andrianteranagna, Mamy; Han, Zhi-Yan; Masliah-Planchon, Julien; Tauziede-Espariat, Arnault; Frah, Magali; Dufour, Christelle; Chauvin, Celine; Bouarich, Rachida; Manriquez, Valeria; Turczinski, Sandrina; Delattre, Olivier; Baulande, Sylvain; Ayrault, Olivier; Servant, Nicolas; Beccaria, Kevin; Dangouloff-Ros, Volodia; Bourdeaut, Franck; Mobark, Nahla Ali; Alharbi, Musa; Ballourah, Walid; Alsultan, Abdulrahman; El Manjomi, Fahad; AlNaqib, Zaid; Al-Banyan, Ayman; Balbaid, Ali Abdullah O; Abedalthagafi, MD, Malak; Erker, Craig; Craig, Brandon; Bailey, Simon; Massimino, Maura; Larouche, Valerie; L Finlay, Jonathan; Kline, Cassie; Michaiel, George; Margol, Ashley; Cohen, Kenneth; Cacciotti, Chantel; Harrods, Virginia; Doris, Kathleen; AbdelBaki, Mohammed; Amayiri, Nisreen; Wang, Zhihong; Hansford, Jordan; Hukin, Juliette; Salloum, Ralph; Hoffman, Lindsay; Muray, Jeffrey; Ginn, Kevin; Zapotocky, Zapotocky; Baroni, Lorena; Ramaswamy, Vijay; Gilheens, Stephen; Aguiera, Dolli; Mazewski, Claire; Shah, Shafqat; Strother, Douglas; Muller, Sabine; Gajjar, Amar; Northcott, Paul; Clifford, Steve; Robinson, Giles; Bouffet, Eric; Lafay-Cousin, Lucie; Soja, Jacqueline; Wilson, Rebekah; Yunker, Alexandra; Aziz-Bose, Rahela; Gordon, Erin; Dieli-Conwright, Christina; Cooney, Tabitha; Dorfer, Christian; Pletschko, Thomas; Seiger, Rene; Chocholous, Monika; Kasprian, Gregor; Roessler, Karl; Kollndorfer, Kathrin; Schöpf, Veronika; Leiss, Ulrike; Slavc, Irene; Prayer, Daniela; Lanzenberger, Rupert; Czech, Thomas; Martin, Brice; Garman, Tyler; Laramee, Madeline; Wang, Amy; Hagen, Natalie; Dahmane, Nadia; Thomas, Craig; Souweidane, Mark; Thompson, Dean; Castle, Jemma; Hicks, Debbie; Schwalbe, Ed; Clifford, Steve; El Beltagy, Mohamed; Enayet, Abdelrahman; Sameh, Rana; Nysom, Karsten; Doz, François; Geoerger, Birgit; Øra, Ingrid; Perreault, Sebastien; Norenberg, Ricarda; Fellous, Marc; De La Cuesta, Esther; Laetsch, Theodore W; van Tilburg, Cornelis M; Bennett, Julie; Nobre, Liana; Sheth, Javal; Ryall, Scott; Fang, Karen; Johnson, Monique; Negm, Logine; Chung, Jiil; Komosa, Martin; Nunes, Nuno M; Fat, Mary Jane Lim; Perry, James; Sahgal, Arjun; Detsky, Jay; Bouffet, Eric; Naz-Hazrati, Lili; Dirks, Peter; Ertl-Wagner, Birgit; Kongkham, Paul; Zadeh, Gelareh; Mason, Warren; Climans, Seth; Cusimano, Michael; Das, Sunit; Gao, Andrew; Tsang, Derek; Nguyen, Lananh; Laperriere, Normand; Keith, Julia; Munoz, David; Tabori, Uri; Hawkins, Cynthia; Cantor, Evan; Ogle, Andrea; Meyer, Ashley; Shatara, Margaret; Brossier, Nicole M; Abdelbaki, Mohamed S; Strahle, Jennifer; Cluster, Andrew; Schwake, Michael; Bruns, Ann-Katrn; Müther, Michael; Stummer, Walter; Tsai, Jessica W; Choi, Jungwhan John; Ouaalam, Hakim; Murrillo, Efrain Aguilar; Yeo, Kee Kiat; Vogelzang, Jayne; Sousa, Cecilia; Woods, Jared K; Ligon, Keith L; Warfield, Simon K; Bandopadhayay, Pratiti; Cooney, Tabitha M; Li, Miao; Du, Shuxu; Sun, Yanling; Wang, Shumei; Wu, Wanshui; Sun, Liming

Evaluation of an EZH2 inhibitor in patient-derived orthotopic xenograft models of pediatric brain tumors alone and in combination with chemo- and radiation therapies

在儿童脑肿瘤患者来源的原位异种移植模型中评估 EZH2 抑制剂单独使用以及与化疗和放疗联合使用的疗效

Qi, Lin; Lindsay, Holly; Kogiso, Mari; Du, Yuchen; Braun, Frank K; Zhang, Huiyuan; Guo, Lei; Zhao, Sibo; Injac, Sarah G; Baxter, Patricia A; Su, Jack Mf; Xiao, Sophie; Erickson, Stephen W; Earley, Eric J; Teicher, Beverly; Smith, Malcolm A; Li, Xiao-Nan

Synergistic anti-tumor efficacy of mutant isocitrate dehydrogenase 1 inhibitor SYC-435 with standard therapy in patient-derived xenograft mouse models of glioma

在胶质瘤患者来源的异种移植小鼠模型中,突变型异柠檬酸脱氢酶 1 抑制剂 SYC-435 与标准疗法具有协同抗肿瘤疗效

Kogiso, Mari; Qi, Lin; Du, Yuchen; Braun, Frank K; Zhang, Huiyuan; Huang, L Frank; Guo, Lei; Huang, Yulun; Teo, Wan-Yee; Lindsay, Holly; Zhao, Sibo; Injac, Sarah G; Liu, Zhen; Mehta, Vidya; Tran, Diep; Li, Feng; Baxter, Patricia A; Su, Jack M; Perlaky, Laszlo; Parsons, D Williams; Chintagumpala, Murali; Adesina, Adekunle; Song, Yongcheng; Li, Xiao-Nan