日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Creation of zebularine-resistant human cytidine deaminase mutants to enhance the chemoprotection of hematopoietic stem cells

构建对泽布拉林耐药的人类胞苷脱氨酶突变体以增强造血干细胞的化学保护作用

Ruan, Hongmei; Qiu, Songbo; Beard, Brian C; Black, Margaret E

(211)Astatine-Conjugated Monoclonal CD45 Antibody-Based Nonmyeloablative Conditioning for Stem Cell Gene Therapy

(211)基于砹偶联单克隆CD45抗体的非清髓性干细胞基因治疗预处理

Burtner, Christopher R; Chandrasekaran, Devikha; Santos, Erlinda B; Beard, Brian C; Adair, Jennifer E; Hamlin, Donald K; Wilbur, D Scott; Sandmaier, Brenda M; Kiem, Hans-Peter

VISA--Vector Integration Site Analysis server: a web-based server to rapidly identify retroviral integration sites from next-generation sequencing

VISA——载体整合位点分析服务器:一个基于网络的服务器,用于从下一代测序数据中快速识别逆转录病毒整合位点。

Hocum, Jonah D; Battrell, Logan R; Maynard, Ryan; Adair, Jennifer E; Beard, Brian C; Rawlings, David J; Kiem, Hans-Peter; Miller, Daniel G; Trobridge, Grant D

Pigtailed macaques as a model to study long-term safety of lentivirus vector-mediated gene therapy for hemoglobinopathies

以豚尾猕猴为模型研究慢病毒载体介导的血红蛋白病基因治疗的长期安全性

Kiem, Hans-Peter; Arumugam, Paritha I; Burtner, Christopher R; Fox, Catherine F; Beard, Brian C; Dexheimer, Phillip; Adair, Jennifer E; Malik, Punam

Positive selection of mC46-expressing CD4+ T cells and maintenance of virus specific immunity in a primate AIDS model.

在灵长类艾滋病模型中,对表达 mC46 的 CD4+ T 细胞进行阳性选择并维持病毒特异性免疫

Younan Patrick M, Polacino Patricia, Kowalski John P, Peterson Christopher W, Maurice Nicholas J, Williams Nathaniel P, Ho On, Trobridge Grant D, Von Laer Dorothee, Prlic Martin, Beard Brian C, DeRosa Stephen, Hu Shiu-Lok, Kiem Hans-Peter

Extended survival of glioblastoma patients after chemoprotective HSC gene therapy

接受化疗保护性造血干细胞基因治疗后,胶质母细胞瘤患者的生存期延长

Adair, Jennifer E; Beard, Brian C; Trobridge, Grant D; Neff, Tobias; Rockhill, Jason K; Silbergeld, Daniel L; Mrugala, Maciej M; Kiem, Hans-Peter

Novel reporter systems for facile evaluation of I-SceI-mediated genome editing

用于简便评估 I-SceI 介导的基因组编辑的新型报告系统

Muñoz, Nina M; Beard, Brian C; Ryu, Byoung Y; Luche, Ralf M; Trobridge, Grant D; Rawlings, David J; Scharenberg, Andrew M; Kiem, Hans-Peter

Cyclophosphamide promotes engraftment of gene-modified cells in a mouse model of Fanconi anemia without causing cytogenetic abnormalities

环磷酰胺可促进基因修饰细胞在范可尼贫血小鼠模型中的植入,且不引起细胞遗传学异常。

Adair, Jennifer E; Zhao, Xin; Chien, Sylvia; Fang, Min; Wohlfahrt, Martin E; Trobridge, Grant D; Taylor, Jason A; Beard, Brian C; Kiem, Hans-Peter; Becker, Pamela S

Large animal models for foamy virus vector gene therapy

用于泡沫病毒载体基因治疗的大型动物模型

Trobridge, Grant D; Horn, Peter A; Beard, Brian C; Kiem, Hans-Peter

Stem cell selection in vivo using foamy vectors cures canine pyruvate kinase deficiency

利用泡沫载体在体内进行干细胞筛选可治愈犬丙酮酸激酶缺乏症

Trobridge, Grant D; Beard, Brian C; Wu, Robert A; Ironside, Christina; Malik, Punam; Kiem, Hans-Peter