日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Patient-derived tumoroids from CIC::DUX4 rearranged sarcoma identify MCL1 as a therapeutic target.

从 CIC::DUX4 重排肉瘤中分离出的患者来源的肿瘤样细胞确定 MCL1 为治疗靶点

Breunis Willemijn, Brack Eva, Ehlers Anna C, Bechtold Ingrid, Kisele Samanta, Wurth Jakob, Mous Lieke, Zabele Dorita, Steffen Fabio, Zahnow Felina, Britschgi Christian, Bankel Lorenz, Rothermundt Christian, Vetter Cornelia, Müller Daniel, Botter Sander, Pauli Chantal, Bode Peter, Rinner Beate, Bourquin Jean-Pierre, Roessler Jochen, Grünewald Thomas G P, Schäfer Beat W, Surdez Didier, Wachtel Marco

Single cell transcriptomic profiling identifies tumor-acquired and therapy-resistant cell states in pediatric rhabdomyosarcoma

单细胞转录组分析鉴定儿童横纹肌肉瘤中肿瘤获得性和治疗耐药性细胞状态

Sara G Danielli #,Yun Wei #,Michael A Dyer,Elizabeth Stewart,Heather Sheppard,Marco Wachtel,Beat W Schäfer,Anand G Patel,David M Langenau

The gray area of RQ-PCR-based measurable residual disease: subdividing the "positive, below quantitative range" category

基于RQ-PCR的可测量残留病灶的灰色地带:细分“阳性,低于定量范围”类别

Kotrova, Michaela; Fronkova, Eva; Svaton, Michael; Drandi, Daniela; Schön, Felix; Hoogeveen, Patricia; Hancock, Jeremy; Skotnicova, Aneta; Schilhabel, Anke; Eckert, Cornelia; Clappier, Emmanuelle; Cazzaniga, Gianni; Schäfer, Beat W; van Dongen, Jacques J M; Ritgen, Matthias; Pott, Christiane; van der Velden, Vincent H J; Trka, Jan; Brüggemann, Monika

Analysis of measurable residual disease by IG/TR gene rearrangements: quality assurance and updated EuroMRD guidelines

通过IG/TR基因重排分析可测量残留病灶:质量保证和更新的EuroMRD指南

van der Velden, Vincent H J; Dombrink, Isabel; Alten, Julia; Cazzaniga, Giovanni; Clappier, Emmanuelle; Drandi, Daniela; Eckert, Cornelia; Fronkova, Eva; Hancock, Jeremy; Kotrova, Michaela; Kraemer, Rebekka; Montonen, Mirkka; Pfeifer, Heike; Pott, Christiane; Raff, Thorsten; Trautmann, Heiko; Cavé, Hélène; Schäfer, Beat W; van Dongen, Jacques J M; Trka, Jan; Brüggemann, Monika

Elimusertib has Antitumor Activity in Preclinical Patient-Derived Pediatric Solid Tumor Models

Elimusertib在临床前患者来源的儿科实体瘤模型中具有抗肿瘤活性

Pusch, Fabian F; Dorado García, Heathcliff; Xu, Robin; Gürgen, Dennis; Bei, Yi; Brückner, Lotte; Röefzaad, Claudia; von Stebut, Jennifer; Bardinet, Victor; Chamorro Gonzalez, Rocío; Eggert, Angelika; Schulte, Johannes H; Hundsdörfer, Patrick; Seifert, Georg; Haase, Kerstin; Schäfer, Beat W; Wachtel, Marco; Kühl, Anja A; Ortiz, Michael V; Wengner, Antje M; Scheer, Monika; Henssen, Anton G

Evaluation of the Role of AXL in Fusion-positive Pediatric Rhabdomyosarcoma Identifies the Small-molecule Inhibitor Bemcentinib (BGB324) as Potent Chemosensitizer

对 AXL 在融合阳性儿童横纹肌肉瘤中的作用进行评估,发现小分子抑制剂 Bemcentinib (BGB324) 是一种有效的化疗增敏剂。

Sara G Danielli ,Jakob Wurth ,Sarah Morice ,Samanta Kisele ,Didier Surdez ,Olivier Delattre ,Peter K Bode ,Marco Wachtel ,Beat W Schäfer

Functional Classification of Fusion Proteins in Sarcoma

肉瘤中融合蛋白的功能分类

Wachtel, Marco; Surdez, Didier; Grünewald, Thomas G P; Schäfer, Beat W

Single-cell profiling of alveolar rhabdomyosarcoma reveals RAS pathway inhibitors as cell-fate hijackers with therapeutic relevance

单细胞分析揭示RAS通路抑制剂作为细胞命运劫持者具有治疗意义,可用于治疗肺泡横纹肌肉瘤。

Sara G Danielli ,Ermelinda Porpiglia ,Andrea J De Micheli ,Natalia Navarro ,Michael J Zellinger ,Ingrid Bechtold ,Samanta Kisele ,Larissa Volken ,Quy A Ngo ,Joana G Marques ,Stephanie Kasper ,Peter K Bode ,Anton G Henssen ,Dennis Gürgen ,Olivier Delattre ,Didier Surdez ,Josep Roma ,Peter Bühlmann ,Helen M Blau ,Marco Wachtel ,Beat W Schäfer

Adult Low-Hypodiploid Acute Lymphoblastic Leukemia Emerges from Preleukemic TP53-Mutant Clonal Hematopoiesis

成人低亚二倍体急性淋巴细胞白血病起源于白血病前期TP53突变克隆性造血

Kim, Rathana; Bergugnat, Hugo; Larcher, Lise; Duchmann, Matthieu; Passet, Marie; Gachet, Stéphanie; Cuccuini, Wendy; Lafage-Pochitaloff, Marina; Pastoret, Cédric; Grardel, Nathalie; Asnafi, Vahid; Schäfer, Beat W; Delabesse, Eric; Itzykson, Raphaël; Adès, Lionel; Hicheri, Yosr; Chalandon, Yves; Graux, Carlos; Chevallier, Patrice; Hunault, Mathilde; Leguay, Thibaut; Huguet, Françoise; Lhéritier, Véronique; Dombret, Hervé; Soulier, Jean; Rousselot, Philippe; Boissel, Nicolas; Clappier, Emmanuelle

Retraction notice to Corrigendum to "Inhibition of HDACs reduces Ewing sarcoma tumor growth through EWS-FLI1 protein destabilization" [Neoplasia 31 (2022) 100805]

撤稿通知:更正“抑制 HDACs 通过 EWS-FLI1 蛋白不稳定化减少尤文氏肉瘤肿瘤生长”[Neoplasia 31 (2022) 100805]

Pedot, Gloria; Marques, Joana Graça; Ambühl, Philip P; Wachtel, Marco; Kasper, Stephanie; Ngo, Quy A; Niggli, Felix K; Schäfer, Beat W